IP Library Granted Patent US 7,491,312
Granted Patent B2
US 7,491,312 · App. 10/696,752 · Granted Feb 17, 2009

Identifying therapeutic compounds based on their physical-chemical properties

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Quick Facts
Patent No.
US 7,491,312
App. No.
10/696,752
Granted
Feb 17, 2009
Kind
B2
Abstract

The present invention is directed to rapid and efficient methods of identifying therapeutic compounds by allowing only the most favorable molecules initially selected based on their physical-chemical profile falling within a range predefined by the physical-chemical/biological relationship of a previously tested small subset of compounds of same core structure to be assayed; and to the therapeutic compositions identified by said methods.

Claims (46)

1. A method of identifying and selecting therapeutic compounds having a predetermined core structure, said method comprising:

establishing a relationship between physical-chemical profile and biological activity; wherein the physical-chemical profile comprises one or more parameters selected from reversibility of one or more oxidation waves or reversibility of one or more reduction waves; and wherein the biological activity is measured in an assay effective in detecting compounds for the treatment of a targeted disorder;

testing further potential therapeutic candidates with said core structure for their physical-chemical properties; and

selecting therapeutic compounds based on their physical-chemical parameters falling within a range predefined by the physical-chemical/biological relationship of the previously tested subset of compounds.

2. The method of claim 1 , wherein the physical-chemical profile comprises the parameter for reversibility of one or more oxidation waves.

3. The method of claim 1 , wherein the physical-chemical profile comprises the parameter for reversibility of one or more reduction waves.

4. The method of claim 3 , wherein the biological activity assay comprises the E-selectin (ELAM) cell based assay detecting compounds with an EC 50 lower than 30 μM versus a silver/silver chloride reference electrode.

5. The method of claim 4 , wherein the therapeutic compound is selected if it comprises a quinone core structure and if its physical-chemical profile comprises a parameter for the total reversibility of reduction of 75% or more.

6. The method of claim 5 , wherein the physical-chemical profile additionally comprises one or more parameters selected from the energy profile parameters and the transport profile parameters.

7. The method of claim 5 wherein the compound is for the treatment of a condition characterized by oxidative stress.

8. The method of claim 1 , wherein the assay is a cell-based assay comprising one or more assays selected from the High Glutamate-Induced Oxidative Stress (HGOS) assay wherein the compounds in the previously tested subset group of compounds have the ability to protect at least 30% of energetically competent cells against stressor induced cell death; and the E-selectin (ELAM) assay wherein the compounds in the previously tested subset group of compounds exhibit an EC 50 lower than about 30 μM.

9. The method of claim 8 , wherein the therapeutic compound is selected if it comprises a stilbene core structure and if its physical-chemical profile comprises one or more parameters selected from the parameter for potential of the first oxidation wave that falls between about 800 mV and 1400 mV versus a silver/silver chloride reference electrode, and the parameter for the reversibility of the first oxidation wave that measures about 20% or more.

10. The method of claim 9 , wherein the physical-chemical profile additionally comprises one or more parameters selected from the energy profile parameters and the transport profile parameters.

11. The method of claim 9 , wherein the therapeutic compound is for the treatment of a condition characterized by oxidative stress.

12. The method of claim 8 , wherein the therapeutic compound is selected if it comprises a core structure of Formula I:

wherein additional substitution at the phenyl rings does not include a nitro group; and if its physical-chemical profile comprises the parameter for potential of the first oxidation wave that falls below 1000 mV versus a silver/silver chloride reference electrode.

13. The method of claim 12 , wherein the physical-chemical profile additionally comprises one or more parameters selected from the energy profile parameters and the transport profile parameters.

14. The method of claim 12 , wherein the therapeutic compound is for the treatment of a condition characterized by oxidative stress.

15. The method of claim 8 , wherein the therapeutic compound is selected if it comprises a core structure of Formula I:

wherein additional substitution at the phenyl rings includes a nitro group; and if its physical-chemical profile comprises one or more parameters selected from the parameter for potential of the first oxidation wave that falls between about 950 mV and 1250 mV versus a silver/silver chloride reference electrode, and the parameter for reversibility of the first oxidation wave measures more than 20%.

16. The method of claim 15 , wherein the physical-chemical profile additionally comprises one or more parameters selected from the energy profile parameters and the transport profile parameters.

17. The method of claim 15 , wherein the therapeutic compound is for the treatment of a condition characterized by oxidative stress.

18. A method of identifying and selecting therapeutic compounds having a predetermined core structure, said method comprising:

establishing a relationship between physical-chemical profile and biological activity; wherein the physical-chemical profile comprises a parameter for onset of oxidation; and wherein the biological activity is measured in an assay comprising the E-selectin (ELAM) cell based assay detecting compounds with an EC 50 lower than 30 μM;

testing further potential therapeutic candidates with said core structure for their physical-chemical properties; and

selecting therapeutic compounds based on their physical-chemical parameters falling within a range predefined by the physical-chemical/biological relationship of the previously tested subset of compounds.

19. The method of claim 18 , wherein the therapeutic compound is selected if it comprises a flavonoid core structure of Formula II:

wherein none of the substituents are hydroxy groups;

and if its physical-chemical profile comprises the parameter for onset of oxidation that falls between about 850 mV and 1050 mV versus a silver/silver chloride reference electrode.

20. The method of claim 19 , wherein the physical-chemical profile additionally comprises one or more parameters selected from the energy profile parameters and the transport profile parameters.

21. The method of claim 19 , wherein the therapeutic compound is for the treatment of a condition characterized by inflammation.

22. The method of claim 18 , wherein the therapeutic compound is selected if it comprises a flavonoid core structure of Formula II:

wherein one or more of the substituents are hydroxy groups;

and if its physical-chemical profile comprises the parameter for onset of oxidation that falls between about 350 mV and 650 mV versus a silver/silver chloride reference electrode.

23. The method of claim 22 , wherein the physical-chemical profile additionally comprises one or more parameters selected from the energy profile parameters and the transport profile parameters.

24. The method of claim 22 , wherein the therapeutic compound is for the treatment of a condition characterized by inflammation.

25. A method of identifying and selecting therapeutic compounds having a predetermined core structure, said method comprising:

establishing a relationship between physical-chemical profile and biological activity; wherein the physical-chemical profile comprises a parameter for potential of oxidation wave; and wherein the biological activity is measured in an assay comprising an HGOS assay protecting at least 30% of the cells against stressor induced cell death;

testing further potential therapeutic candidates with said core structure for their physical-chemical properties; and

selecting therapeutic compounds based on their physical-chemical parameters falling within a range predefined by the physical-chemical/biological relationship of the previously tested subset of compounds.

26. The method of claim 25 , wherein the therapeutic compound is selected if it comprises a flavonoid core structure and if its physical-chemical profile comprises the parameter for oxidation potential that falls between about 1050 mV and 1450 mV versus a silver/silver chloride reference electrode.

27. The method of claim 26 , wherein the physical-chemical profile additionally comprises one or more parameters selected from the energy profile parameters and the transport profile parameters.

28. The method of claim 26 , wherein the therapeutic compound is for the treatment of a condition characterized by oxidative stress.

29. The method of claim 25 , wherein the therapeutic compound is selected if it comprises a chroman core structure of Formula IV,

and if its physical-chemical profile comprises the parameter for oxidation potential that falls between about 850 mV and 1200 mV versus a silver/silver chloride reference electrode.

30. The method of claim 29 , wherein the physical-chemical profile additionally comprises one or more parameters selected from the energy profile parameters and the transport profile parameters.

Assignments (6)
TERMINATION AND RELEASE OF PATENT SECURITY AGREEMENT @ REEL 061803 AND FRAME 0878 Recorded Oct 20, 2023
From: WILMINGTON TRUST, NATIONAL ASSOCIATION, AS ADMINISTRATIVE AGENT
To: PTC THERAPEUTICS, INC.
Reel/Frame 065303/0163 →
SECURITY INTEREST Recorded Oct 28, 2022
From: PTC THERAPEUTICS, INC.
To: WILMINGTON TRUST, NATIONAL ASSOCIATION
Reel/Frame 061803/0878 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Nov 15, 2019
From: BIOELECTRON TECHNOLOGY CORPORATION
To: PTC THERAPEUTICS, INC.
Reel/Frame 051041/0478 →
CHANGE OF NAME Recorded Feb 8, 2017
From: EDISON PHARMACEUTICALS, INC.
To: BIOELECTRON TECHNOLOGY CORPORATION
Reel/Frame 041660/0644 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Sep 3, 2015
From: AMPERE LIFE SCIENCES, INC.
To: EDISON PHARMACEUTICALS, INC.
Reel/Frame 036491/0693 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Mar 1, 2012
From: EDISON PHARMACEUTICALS, INC.
To: AMPERE LIFE SCIENCES, INC.
Reel/Frame 027792/0432 →