IP Library Granted Patent US 8,921,376
Granted Patent B2
US 8,921,376 · App. 11/438,748 · Granted Dec 30, 2014

Pyrrolopyridines useful as inhibitors of protein kinase

Inventors: Mark Ledeboer (Acton, MA); Marion Wannamaker (Stow, MA); Luc Farmer (Foxboro, MA); Tiansheng Wang (Concord, MA); Albert Pierce (Cambridge, MA); Gabriel Martinez-Botella (West Roxbury, MA); Randy Bethiel (Lexington, MA); Guy Bemis (Arlington, MA); Jian Wang (Newton, MA); Francesco Salituro (Marlboro, MA); Michael Arnost (North Andover, MA); Jon Come (Cambridge, MA); Jeremy Green (Waltham, MA); Michelle Stewart (Somerville, MA); Craig Marhefka (Rockville, MD)
Assignee: Vertex Pharmaceuticals Incorporated
C07D471/04C07D487/04
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Quick Facts
Patent No.
US 8,921,376
App. No.
11/438,748
Granted
Dec 30, 2014
Kind
B2
Abstract

The present invention relates to compounds useful as inhibitors of protein kinases, particularly of JAK family and ROCK family kinases. The invention also provides pharmaceutically acceptable compositions comprising said compounds and methods of using the compositions in the treatment of various disease, conditions, or disorders.

Claims (62)

1. A compound of formula I

or a pharmaceutically acceptable salt thereof

wherein

Q is

Z is a bond, NH, N(C 1-3 aliphatic) or C═CH 2 ;

R 1 is —(C 1-2 aliphatic) p -R 4 wherein each R 1 is optionally substituted with 1-3 occurrences of J;

R 2 is —(C 1-2 aliphatic) d -R 5 wherein each R 2 is optionally substituted with 1-3 occurrences of J;

R 3 is halogen, —CN, —NO 2 or —(U) m —X, wherein

U is a C 1-6 aliphatic, wherein up to two methylene units are optionally and independently replaced by G U and wherein U is optionally substituted with 1-4 J U ;

X is H, halogen, CN, NO 2 , S(O)R, SO 2 R, C 1-4 haloaliphatic, or a group selected from C 1-6 aliphatic, a C 3-10 cycloaliphatic, C 6-10 aryl, 5-10 membered heteroaryl, 5-10 membered heterocyclyl; wherein said group is optionally substituted with 1-4 J X ;

G U is —NH—, —NR—, —O—, —S—, —CO 2 —, —OC(O)—, —C(O)CO—, —C(O)—, —C(O)NH—, —C(O)NR—, —C(═N—CN)—, —NHCO—, —NRCO—, —NHC(O)O—, —NRC(O)O—, —SO 2 NH—, —SO 2 NR—, —NHSO 2 —, —NRSO 2 —, —NHC(O)NH—, —NRC(O)NH—, —NHC(O)NR—, —NRC(O)NR, —OC(O)NH—, —OC(O)NR—, —NHSO 2 NH—, —NRSO 2 NH—, —NHSO 2 NR—, —NRSO 2 NR—, —SO—, or —SO 2 —;

R 4 is H, halogen, CN, NH 2 , NO 2 , CF 3 , C 1-3 aliphatic, cyclopropyl, NCH 3 , OCH 3 , —C(═O)NH 2 , —C(═O)CH 3 , —NC(═O)CH 3 , or OH;

R 5 is H, halogen, CN, NH 2 , NO 2 , CF 3 , C 1-3 aliphatic, cyclopropyl, NCH 3 , OCH 3 , —C(═O)NH 2 , —C(═O)CH 3 , —NC(═O)CH 3 , or OH;

R is an optionally substituted group selected from C 1-6 aliphatic, C 3-10 cycloaliphatic, C 6-10 aryl, 5-10 membered heteroaryl, or 5-10 membered heterocyclyl; or two R groups, on the same substituent or different substituents, together with the atom(s) to which each R group is bound, form an optionally substituted 3-8 membered heterocyclyl; wherein each R group is independently and optionally substituted with 1-4 occurrences of J R ;

J U , J X , and J R are each independently selected from halogen, L, -(L n )—R′, -(L n )—N(R′) 2 , -(L n )-SR′, -(L n )-OR′, -(L n )-(C 3-10 cycloaliphatic), -(L n )-(C 6-10 aryl), -(L n )-(5-10 membered heteroaryl), -(L n )-(5-10 membered heterocyclyl), oxo, C 1-4 haloalkoxy, C 1-4 haloalkyl, -(L n )-NO 2 , -(L n )-CN, -(L n )-OH, -(L n )-CF 3 , —CO 2 R′, —CO 2 H, —COR′, —COH, —OC(O)R′, or —NC(O)R′; or two J U , J X , or J R groups, on the same substituent or different substituents, together with the atom(s) to which each J U , J X , and J R group is bound, form a 5-7 membered saturated, unsaturated, or partially saturated ring;

J Q is each independently selected from R″, —CH 2 R″, halogen, —CN, —NO 2 , —N(R′)R″, —CH 2 N(R′)R″, —OR″, —CH 2 OR″, —SR″, —CH 2 SR″, —COOR″, —NR′COR″, —NR′COCH 2 R″, —NR′CO(CH 2 ) 2 R″, —NR′COOR″, —CON(R′)R″, —SO 2 N(R′)R″, —CONR′(CH 2 ) 2 N(R′)R″, —CONR(CH 2 ) 3 N(R′)R″, —CONR′(CH 2 ) 4 N(R′)R″, —O(CH 2 ) 2 OR″, O(CH 2 ) 3 OR″, O(CH 2 ) 4 OR″, —O(CH 2 ) 2 N(R′)R″, —O(CH 2 ) 3 N(R)R″, —O(CH 2 ) 4 N(R′)R″, —NR′CH(CH 2 OR 8 )R″, —NR′CH(CH 2 CH 2 OR 8 )R″, —NR′CH(CH 3 )R″, NR′CH(CF 3 )R″, —NR′CH(CH 3 )C(O)OR″, —NR′CH(CF 3 )C(O)OR″, —NR′(CH 2 )R″, —NR′(CH 2 ) 2 R″, —NR′(CH 2 ) 3 R″, —NR′(CH 2 ) 4 R″, —NR′(CH 2 )N(R′)R″, —NR′(CH 2 ) 2 N(R′)R″, —NR′(CH 2 ) 3 N(R′)R″, —NR′(CH 2 ) 4 N(R)R″, —NR′(CH 2 )OR″, —NR′(CH 2 ) 2 OR″, —NR′(CH 2 ) 3 OR″, —NR′(CH 2 ) 4 OR″, —NR′CH(CH 2 CH 3 )R″, —NR′CH 2 C(O)N(R′)R″, —NR′CH(CH 3 )C(O)N(R′)R″, NR′CH(CF 3 )C(O)N(R)R″, —NR′CH(CH 2 CH 3 )C(O)N(R′)R″, —NR′CH(CH(CH 3 ) 2 )C(O)N(R′)R″, —NR′CH(C(CH 3 ) 3 )C(O)N(R′)R″, —NR′CH(CH 2 CH(CH 3 ) 2 )C(O)N(R′)R″, —NR′CH(CH 2 OR 8 )C(O)N(R′)R″ or —NR′CH(CH 2 CH 2 N(Me) 2 )C(O)N(R′)R″;

R 8 is H or C 1-6 alkyl;

R′ is H or C 1-6 aliphatic; or two R′ groups, together with the atom to which they are attached, optionally form a 3-6 membered cycloaliphatic or heterocyclyl, wherein said aliphatic, cycloaliphatic or heterocyclyl is optionally substituted with R*, —OR*, —SR*, —NO 2 , —CF 3 , —CN, —CO 2 R*, —COR*, OCOR*, NHCOR*, wherein R* is H or C 1-6 aliphatic;

R″ is H, or is an optionally substituted group selected from C 1-6 aliphatic, C 3-10 cycloaliphatic, C 6-10 aryl, 5-10 membered heteroaryl, or 5-10 membered heterocyclyl; or two R″ groups, on the same substituent or different substituents, together with the atom(s) to which each R″ group is bound, form an optionally substituted 3-8 membered heterocyclyl; wherein each optionally substituted R″ group is independently and optionally substituted with 1-6 occurrences of J R ;

L is a C 1-6 aliphatic wherein up to three methylene units are replaced by —NH—, —NR 6 —, —O—, —S—, —CO 2 —, —OC(O)—, —C(O)CO—, —C(O)—, —C(O)NH—, —C(O)NR 6 —, —C(═N—CN), —NHCO—, —NR 6 CO—, —NHC(O)O—, —NR 6 C(O)O—, —SO 2 NH—, —SO 2 NR 6 —, —NHSO 2 —, —NR 6 SO 2 —, —NHC(O)NH—, —NR 6 C(O)NH—, —NHC(O)NR 6 —, —NR 6 C(O)NR 6 , —OC(O)NH—, —OC(O)NR 6 —, —NHSO 2 NH—, —NR 6 SO 2 NH—, —NHSO 2 NR 6 —, —NR 6 SO 2 NR 6 —, —SO—, or —SO 2 —;

R 6 is selected from C 1-6 aliphatic, C 3-10 cycloaliphatic, C 6-10 aryl, 5-10 membered heteroaryl, or 5-10 membered heterocyclyl; or two R 6 groups, on the same substituent or different substituents, together with the atom(s) to which each R 6 group is bound, form a 3-8 membered heterocyclyl;

J is halogen, OCH 3 , OH, NO 2 , NH 2 , SCH 3 , NCH 3 , CN, unsubstituted C 1-2 aliphatic; two J's, together with the carbon to which they are attached, form a cyclopropyl ring or C═O; and

m, n, d, and p are each independently 0 or 1.

2. A compound of formula I-a

or a pharmaceutically acceptable salt thereof

wherein

Q is

R 1 is —(C 1-2 aliphatic) p -R 4 wherein each R 1 is optionally substituted with 1-3 occurrences of J;

R 2 is —(C 1-2 aliphatic) d -R 5 wherein each R 2 is optionally substituted with 1-3 occurrences of J;

R 3 is halogen, —CN, —NO 2 or —(U) m —X, wherein

U is a C 1-6 aliphatic, wherein up to two methylene units are optionally and independently replaced by G U and wherein U is optionally substituted with 1-4 J U ;

X is H, halogen, CN, NO 2 , S(O)R, SO 2 R, C 1-4 haloaliphatic, or a group selected from C 1-6 aliphatic, a C 3-10 cycloaliphatic, C 6-10 aryl, 5-10 membered heteroaryl, 5-10 membered heterocyclyl; wherein said group is optionally substituted with 1-4 J X ;

G U is —NH—, —NR—, —O—, —S—, —CO 2 —, —OC(O)—, —C(O)CO—, —C(O)—, —C(O)NH—, —C(O)NR—, —C(═N—CN)—, —NHCO—, —NRCO—, —NHC(O)O—, —NRC(O)O—, —SO 2 NH—, —SO 2 NR—, —NHSO 2 —, —NRSO 2 —, —NHC(O)NH—, —NRC(O)NH—, —NHC(O)NR—, —NRC(O)NR, —OC(O)NH—, —OC(O)NR—, —NHSO 2 NH—, —NRSO 2 NH—, —NHSO 2 NR—, —NRSO 2 NR—, —SO—, or —SO 2 —;

R 4 is H, halogen, CN, NH 2 , NO 2 , CF 3 , C 1-3 aliphatic, cyclopropyl, NCH 3 , OCH 3 , —C(═O)NH 2 , —C(═O)CH 3 , —NC(═O)CH 3 , or OH;

R 5 is H, halogen, CN, NH 2 , NO 2 , CF 3 , C 1-3 aliphatic, cyclopropyl, NCH 3 , OCH 3 , —C(═O)NH 2 , —C(═O)CH 3 , —NC(═O)CH 3 , or OH;

R is an optionally substituted group selected from C 1-6 aliphatic, C 3-10 cycloaliphatic, C 6-10 aryl, 5-10 membered heteroaryl, or 5-10 membered heterocyclyl; or two R groups, on the same substituent or different substituents, together with the atom(s) to which each R group is bound, form an optionally substituted 3-8 membered heterocyclyl; wherein each R group is independently and optionally substituted with 1-4 occurrences of J R ;

J U , J X , and J R are each independently selected from halogen, L, -(L n )-R′, -(L n )-N(R′) 2 , -(L n )-SR′, -(L n )-OR′, -(L n )-(C 3-10 cycloaliphatic), -(L n )-(C 6-10 aryl), -(L n )-(5-10 membered heteroaryl), -(L n )-(5-10 membered heterocyclyl), oxo, C 1-4 haloalkoxy, C 1-4 haloalkyl, -(L n )-NO 2 , -(L n )-CN, -(L n )-OH, -(L n )-CF 3 , —CO 2 R′, —CO 2 H, —COR′, —COH, —OC(O)R′, or —NC(O)R′; or two J U , J X , or J R groups, on the same substituent or different substituents, together with the atom(s) to which each J U , J X , and J R group is bound, form a 5-7 membered saturated, unsaturated, or partially saturated ring;

J Q is each independently selected from R″, —CH 2 R″, halogen, —CN, —NO 2 , —N(R′)R″, —CH 2 N(R′)R″, —OR″, —CH 2 OR″, —SR″, —CH 2 SR″, —COOR″, —NR′COR″, —NR′COCH 2 R″, —NR′CO(CH 2 ) 2 R″, —NR′COOR″, —CON(R′)R″, —SO 2 N(R′)R″, —CONR′(CH 2 ) 2 N(R)R″, —CONR(CH 2 ) 3 N(R′)R″—CONR′(CH 2 ) 4 N(R′)R″, —O(CH 2 ) 2 OR″, O(CH 2 ) 3 OR″, O(CH 2 ) 4 OR″, —O(CH 2 ) 2 N(R′)R″, —O(CH 2 ) 3 N(R)R″, —O(CH 2 ) 4 N(R)R″, —NR′CH(CH 2 OR 8 )R″, —NR′CH(CH 2 CH 2 OR 8 )R″, —NR′CH(CH 3 )R″, NR′CH(CF 3 )R″, —NR′CH(CH 3 )C(O)OR″, —NR′CH(CF 3 )C(O)OR″, —NR′(CH 2 )R″, —NR′(CH 2 ) 2 R″, —NR′(CH 2 ) 3 R″, —NR′(CH 2 ) 4 R″, —NR′(CH 2 )N(R′)R″, —NR′(CH 2 ) 2 N(R′)R″, —NR′(CH 2 ) 3 N(R′)R″, —NR′(CH 2 ) 4 N(R)R″, —NR′(CH 2 )OR″, —NR′(CH 2 ) 2 OR″, —NR′(CH 2 ) 3 OR″, —NR′(CH 2 ) 4 OR″, —NR′CH(CH 2 CH 3 )R″, —NR′CH 2 C(O)N(R′)R″, —NR′CH(CH 3 )C(O)N(R′)R″, NR′CH(CF 3 )C(O)N(R′)R″, —NR′CH(CH 2 CH 3 )C(O)N(R′)R″, —NR′CH(CH(CH 3 ) 2 )C(O)N(R′)R″, —NR′CH(C(CH 3 ) 3 )C(O)N(R′)R″, —NR′CH(CH 2 CH(CH 3 ) 2 )C(O)N(R′)R″, —NR′CH(CH 2 OR 8 )C(O)N(R′)R″ or —NR′CH(CH 2 CH 2 N(Me) 2 )C(O)N(R′)R″;

R 8 is H or C 1-6 alkyl;

R′ is H or C 1-6 aliphatic; or two R′ groups, together with the atom to which they are attached, optionally form a 3-6 membered cycloaliphatic or heterocyclyl, wherein said aliphatic, cycloaliphatic or heterocyclyl is optionally substituted with R*, —OR*, —SR*, —NO 2 , —CF 3 , —CN, —CO 2 R*, —COR*, OCOR*, NHCOR*, wherein R* is H or C 1-6 aliphatic;

R″ is H, or is an optionally substituted group selected from C 1-6 aliphatic, C 3-10 cycloaliphatic, C 6-10 aryl, 5-10 membered heteroaryl, or 5-10 membered heterocyclyl; or two R″ groups, on the same substituent or different substituents, together with the atom(s) to which each R″ group is bound, form an optionally substituted 3-8 membered heterocyclyl; wherein each optionally substituted R″ group is independently and optionally substituted with 1-6 occurrences of J R ;

L is a C 1-6 aliphatic wherein up to three methylene units are replaced by —NH—, —NR 6 —, —O—, —S—, —CO 2 —, —OC(O)—, —C(O)CO—, —C(O)—, —C(O)NH—, —C(O)NR 6 —, —C(═N—CN), —NHCO—, —NR 6 CO—, —NHC(O)O—, —NR 6 C(O)O—, —SO 2 NH—, —SO 2 NR 6 —, —NHSO 2 —, —NR 6 SO 2 —, —NHC(O)NH—, —NR 6 C(O)NH—, —NHC(O)NR 6 —, —NR 6 C(O)NR 6 , —OC(O)NH—, —OC(O)NR 6 —, —NHSO 2 NH—, —NR 6 SO 2 NH—, —NHSO 2 NR 6 —, —NR 6 SO 2 NR 6 —, —SO—, or —SO 2 —;

R 6 is selected from C 1-6 aliphatic, C 3-10 cycloaliphatic, C 6-10 aryl, 5-10 membered heteroaryl, or 5-10 membered heterocyclyl; or two R 6 groups, on the same substituent or different substituents, together with the atom(s) to which each R 6 group is bound, form a 3-8 membered heterocyclyl;

J is halogen, OCH 3 , OH, NO 2 , NH 2 , SCH 3 , NCH 3 , CN, unsubstituted C 1-2 aliphatic; two J's, together with the carbon to which they are attached, form a cyclopropyl ring or C═O;

m, n, d, and p are each independently 0 or 1.

3. The compound according to claim 1 , wherein R 1 is H, halogen, CN, NH 2 , NO 2 , CF 3 , CH 3 , NCH 3 , OCH 3 , or OH.

4. The compound according to claim 1 , wherein R 2 is H, halogen, CN, NH 2 , NO 2 , CF 3 , CH 3 , NCH 3 , OCH 3 , or OH.

5. The compound according to claim 1 , wherein m is 0 and R 3 is H, halogen, —CN, —NO 2 or X.

6. The compound according to claim 1 , wherein m is 1 and U is an optionally substituted C 1-3 aliphatic, wherein up to two methylene units are optionally replaced with 0-2 G U groups.

7. A compound selected from any one of the following compounds:

8. A pharmaceutical composition comprising the compound according to claim 1 , and a pharmaceutically acceptable carrier, adjuvant, or vehicle.

9. A method of inhibiting ROCK kinase activity or JAK kinase activity in an ex vivo biological sample, comprising contacting said biological sample with a compound according to claim 1 , or with a composition comprising said compound.

10. A method of inhibiting ROCK kinase activity or JAK kinase activity in a patient having rheumatoid arthritis, comprising administering to said patient a compound according to claim 1 , or with a composition comprising said compound.

11. A method of treating or lessening the severity of rheumatoid arthritis in a patient, comprising the step of administering to said patient a compound according to claim 1 , or with a composition comprising said compound.

12. A pharmaceutical composition comprising the compound according to claim 2 , and a pharmaceutically acceptable carrier, adjuvant, or vehicle.

13. A method of inhibiting ROCK kinase activity or JAK kinase activity in an ex vivo biological sample, comprising contacting said biological sample with a compound according to claim 2 , or with a composition comprising said compound.

14. A method of inhibiting ROCK kinase activity or JAK kinase activity in a patient having rheumatoid arthritis, comprising administering to said patient a compound according to claim 2 , or with a composition comprising said compound.

15. A method of treating or lessening the severity of rheumatoid arthritis in a patient, comprising the step of administering to said patient a compound according to claim 2 , or with a composition comprising said compound.

16. A pharmaceutical composition comprising the compound according to claim 7 , and a pharmaceutically acceptable carrier, adjuvant, or vehicle.

17. A method of inhibiting ROCK kinase activity or JAK kinase activity in an ex vivo biological sample, comprising contacting said biological sample with a compound according to claim 7 , or with a composition comprising said compound.

18. A method of inhibiting ROCK kinase activity or JAK kinase activity in a patient having rheumatoid arthritis, comprising administering to said patient a compound according to claim 7 , or with a composition comprising said compound.

19. A method of treating or lessening the severity of rheumatoid arthritis in a patient, comprising the step of administering to said patient a compound according to claim 7 , or with a composition comprising said compound.

Assignments (3)
RELEASE OF SECURITY INTEREST Recorded Oct 14, 2016
From: MACQUARIE US TRADING LLC
To: VERTEX PHARMACEUTICALS INCORPORATED; VERTEX PHARMACEUTICALS (SAN DIEGO) LLC
Reel/Frame 040357/0001 →
SECURITY INTEREST Recorded Jul 10, 2014
From: VERTEX PHARMACEUTICALS INCORPORATED; VERTEX PHARMACEUTICALS (SAN DIEGO) LLC
To: MACQUARIE US TRADING LLC
Reel/Frame 033292/0311 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Sep 22, 2008
From: LEDEBOER, MARK; WANNAMAKER, MARION; FARMER, LUC; WANG, TIANSHENG; PIERCE, ALBERT; BETHIEL, RANDY; BEMIS, GUY; WANG, JIAN; BOTELLA, GABRIEL MARTINEZ; SALITURO, FRANCESCO; ARNOST, MICHAEL; COME, JOHN; GREEN, JEREMY; STEWART, MICHELLE; MARHEFKA, CRAIG
To: VERTEX PHARMACEUTICALS INCORPORATED
Reel/Frame 021563/0251 →
Continuity (2)
Provisional Application 60683554 · May 20, 2005
Related Publication 20070135466A1 · Jun 14, 2007