IP Library Granted Patent US 9,458,214
Granted Patent B2
US 9,458,214 · App. 13/626,207 · Granted Oct 4, 2016

Dual function fibroblast growth factor 21 proteins

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Quick Facts
Patent No.
US 9,458,214
App. No.
13/626,207
Granted
Oct 4, 2016
Kind
B2
Abstract

The present invention relates to dual function fusions proteins comprising fibroblast growth factor 21 (FGF21) and Exenatide, Exendin-4, or GLP-1. Also disclosed are methods for treating FGF21-associated disorders, GLP-1-associated disorders, and Exendin-4-associated disorders, including metabolic conditions.

Claims (24)

1. A dual function fusion protein comprising a GLP-1 receptor agonist, a FGF21 receptor agonist, and an Fc domain, attached to each other via a GS linker, and having an orientation of N-terminus-GLP-1 receptor agonist-linker-Fc domain-linker-FGF21 receptor agonist-C-terminus.

2. The dual function fusion protein of claim 1 , wherein said protein comprises the amino acid sequence of SEQ ID NO:36.

3. The dual function fusion protein of claim 1 , wherein said protein comprises the amino acid sequence of SEQ ID NO:134.

4. The dual function fusion protein of claim 1 , wherein said protein comprises the amino acid sequence of SEQ ID NO:135.

5. The dual function fusion protein of claim 1 , wherein the GLP-1 receptor agonist is selected from wild-type GLP-1, Exendin-4, GLP-1 variants, and Exendin-4 analogues.

6. The dual function fusion protein of claim 5 , wherein the GLP-1 receptor agonist is selected from Exendin-4 and Exendin-4 analogues.

7. The dual function fusion protein of claim 1 , wherein the FGF21 receptor agonist is selected from wild-type FGF21, FGF21 fragments, and FGF21 variants.

8. The dual function fusion protein of claim 7 , wherein the FGF21 receptor agonist is selected from FGF21 variants comprising the following amino acid sequences:

(a) DSSPLLQFGG QVRQRYLYTD DAQETEAHLE IREDGTVGGA AHQSPESLLE LKALKPGVIQ ILGVKTSRFL CQKPDGALYG SLHFDPEACS FRELLLEDGY NVYQSEAHGL PLHLPGNRSP HCDPAPQGPA RFLPLPGLPP ALPEPPGILA PQPPDVGSSD PLAMVGPSQG RSPSYAS (SEQ ID NO: 185);

(b) DSSPLLQFGG QVRQRYLYTD DAQETEAHLE IREDGTVGGA AHQSPESLLE LKALKPGVIQ ILGVKTSRFL CQKPDGALYG SLHFDPEACS FRELLLEDGY NVYQSEAHGL PLHLPGNRSP HCDPAPQGPA RFLPLPGLPP ALPEPPGILA PQPPDVGSSD PLAMVGGSQG RSPSYAS (SEQ ID NO: 186);

(c) D SSPLLQFGGQ VRQRYLYTDD ACQTEAHLEI REDGTVGGAA DQSPESLLQL KALKPGVIQI LGVKTSRFLC QRPDGTLYGS LHFDPEACSF RELLLEDGYN VYQSEAHGLP LHLPCNRSPH RDPASRGPAR FLPLPGLPPA LPEPPGILAP QPPDVGSSDP LAMVGGSQAR SPSYAS (SEQ ID NO: 187); and

(d) D SSPLLQFGGQ VRQRYLYTDD ACQTEAHLEI REDGTVGGAA DQSPESLLQL KALKPGVIQI LGVKTSRFLC QKPDGALYGS LHFDPEACSF RELLLEDGYN VYQSEAHGLP LHLPCNRSPH RDPASRGPAR FLPLPGLPPA LPEPPGILAP QPPDVGSSDP LAMVGGSQAR SPSYAS (SEQ ID NO: 188).

9. A pharmaceutical composition comprising a pharmaceutically acceptable carrier and a therapeutically effective amount of a dual function fusion protein comprising a GLP-1 receptor agonist, a FGF21 receptor agonist, and an Fc domain, attached to each other via a GS linker, and having an orientation of N-terminus-GLP-1 receptor agonist-linker-Fc domain-linker-FGF21 receptor agonist-C-terminus.

10. The pharmaceutical composition of claim 9 , wherein the GLP-1 receptor agonist is selected from wild-type GLP-1, Exendin-4, GLP-1 variants, and Exendin-4 analogues.

11. The pharmaceutical composition of claim 10 , wherein the GLP-1 receptor agonist is selected from Exendin-4 and Exendin-4 analogues.

12. The pharmaceutical composition of claim 9 , wherein the FGF21 receptor agonist is selected from wild-type FGF21, FGF21 fragments, and FGF21 variants.

13. The pharmaceutical composition of claim 12 , wherein the FGF21 receptor agonist is selected from FGF21 variants comprising the following amino acid sequences:

(a) DSSPLLQFGG QVRQRYLYTD DAQETEAHLE IREDGTVGGA AHQSPESLLE LKALKPGVIQ ILGVKTSRFL CQKPDGALYG SLHFDPEACS FRELLLEDGY NVYQSEAHGL PLHLPGNRSP HCDPAPQGPA RFLPLPGLPP ALPEPPGILA PQPPDVGSSD PLAMVGPSQG RSPSYAS (SEQ ID NO: 185);

(b) DSSPLLQFGG QVRQRYLYTD DAQETEAHLE IREDGTVGGA AHQSPESLLE LKALKPGVIQ ILGVKTSRFL CQKPDGALYG SLHFDPEACS FRELLLEDGY NVYQSEAHGL PLHLPGNRSP HCDPAPQGPA RFLPLPGLPP ALPEPPGILA PQPPDVGSSD PLAMVGGSQG RSPSYAS (SEQ ID NO: 186);

(c) D SSPLLQFGGQ VRQRYLYTDD ACQTEAHLEI REDGTVGGAA DQSPESLLQL KALKPGVIQI LGVKTSRFLC QRPDGTLYGS LHFDPEACSF RELLLEDGYN VYQSEAHGLP LHLPCNRSPH RDPASRGPAR FLPLPGLPPA LPEPPGILAP QPPDVGSSDP LAMVGGSQAR SPSYAS (SEQ ID NO: 187); and

(d) D SSPLLQFGGQ VRQRYLYTDD ACQTEAHLEI REDGTVGGAA DQSPESLLQL KALKPGVIQI LGVKTSRFLC QKPDGALYGS LHFDPEACSF RELLLEDGYN VYQSEAHGLP LHLPCNRSPH RDPASRGPAR FLPLPGLPPA LPEPPGILAP QPPDVGSSDP LAMVGGSQAR SPSYAS (SEQ ID NO: 188).

14. The pharmaceutical composition of claim 9 , wherein said protein comprises the amino acid sequence of SEQ ID NO:36.

15. The pharmaceutical composition of claim 9 , wherein said protein comprises the amino acid sequence of SEQ ID NO:134.

16. The pharmaceutical composition of claim 9 , wherein said protein comprises the amino acid sequence of SEQ ID NO:135.

Assignments (6)
MERGER Recorded Apr 22, 2015
From: IRM LLC
To: NOVARTIS INTERNATIONAL PHARMACEUTICAL LTD.
Reel/Frame 035469/0260 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Apr 22, 2015
From: NOVARTIS INTERNATIONAL PHARMACEUTICAL LTD.
To: NOVARTIS AG
Reel/Frame 035469/0858 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Nov 12, 2012
From: BOETTCHER, BRIAN R.; CAPLAN, SHARI L.; DANIELS, DOUGLAS S.; HAMAMATSU, NORIO; LICHT, STUART; LOEW, ANDREAS; WELDON, STEPHEN CRAIG
To: NOVARTIS INSTITUTES FOR BIOMEDICAL RESEARCH, INC.
Reel/Frame 029279/0433 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Nov 12, 2012
From: NOVARTIS INSTITUTES FOR BIOMEDICAL RESEARCH, INC.
To: NOVARTIS AG
Reel/Frame 029279/0603 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Nov 12, 2012
From: CELLITTI, SUSAN E.; GEIERSTANGER, BERNHARD H.
To: NOVARTIS INSTITUTE FOR FUNCTIONAL GENOMICS, INC.
Reel/Frame 029279/0787 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Nov 12, 2012
From: NOVARTIS INSTITUTE FOR FUNCTIONAL GENOMICS, INC.
To: IRM LLC
Reel/Frame 029279/0834 →