IP Library Patent Application 14407054
Patent Application
App. No. 14/407,054

OPTICAL REGULATION OF GENE EXPRESSION IN THE RETINA

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Patent No.
US None
App. No.
14/407,054
Abstract

The present invention provides methods and compositions for regulating transgene expression in a subject using heat generated by electro-magnetic radiation in a target cell. The heat is generated by a thermo generator resided in the target cell upon application the electromagnetic radiation. The amount of the heat is controlled by the energy delivered by the electromagnetic radiation.

Claims (31)

1 . A method for modulating gene expression in a subject, comprising;

(a) expressing a transgene in a plurality of cells in a subject, wherein said plurality of cells comprises a target cell, wherein said target cell comprises;

(i) a polynucleotide encoding said transgene; and

(ii) a thermo generator capable of generating heat upon application of an electromagnetic radiation; and

(b) applying said electromagnetic radiation to said target cell to destroy said target cell, thereby modulating expression of said transgene in said subject.

2 . The method of claim 1 , wherein said target cell is a pigmented cell and said thermo generator comprises a chromophore or pigment.

3 . The method of claim 2 , wherein said pigmented cell is selected from the group consisting of: retinal pigment epithelium, iris epithelium, trabecular meshwork epithelium, and a cell in the pigmented choroid.

4 .- 10 . (canceled)

11 . The method of claim 1 , wherein said electromagnetic radiation is produced by a laser.

12 . The method of claim 11 , wherein said laser has a beam width of less than 1 mm.

13 . The method of claim 11 , wherein said laser has a power of about 500 mW to 5,000 mW.

14 . The method of claim 1 , wherein said electromagnetic radiation is applied by one or more pulses.

15 . The method of claim 14 , wherein the duration of said pulse of electromagnetic radiation is less than 100 μs.

16 . The method of claim 1 , wherein said electromagnetic radiation is applied by scanning a beam of electromagnetic radiation.

17 . (canceled)

18 . The method of claim 16 , wherein the scanning beam has a dwell time less than 100 μs.

19 . A method for modulating gene expression in a target cell by electromagnetic radiation, comprising;

(a) expressing a transgene in a target cell, wherein said target cell comprises:

(i) a polynucleotide encoding heat-responsive promoter that controls expression of said transgene; and

(ii) a thermo generator that is capable of generating heat upon application of an electromagnetic radiation; and

(b) applying said electromagnetic radiation to said target cell to increase the expression of said transgene.

20 . The method of claim 19 , wherein said target cell is a pigmented cell and said thermo generator comprise a chromophore or pigment.

21 . The method of claim 19 , wherein said pigmented cell is selected from the group consisting of: retinal pigment epithelium, iris epithelium, trabecular meshwork epithelium, and a cell in the pigmented choroid.

22 .- 28 . (canceled)

29 . The method of claim 19 , wherein said electromagnetic radiation is a laser.

30 . The method of claim 29 , wherein said laser has a beam width of less than 1 mm.

31 . The method of claim 29 , wherein said laser has a power of about 5 mW to 500 mW.

32 . The method of claim 19 , wherein said electromagnetic radiation is applied by one or more pulses.

33 . The method of claim 32 , wherein the duration of applying said pulses of electromagnetic radiation is less than 100 μs.

34 . The method of claim 19 , wherein said electromagnetic radiation is applied by scanning a beam of electromagnetic radiation.

35 . The method of claim 34 , wherein the scanning beam has a dwell time less than 100 μs.

Assignments (3)
CHANGE OF NAME Recorded Jun 21, 2016
From: AVALANCHE BIOTECHNOLOGIES, INC.
To: ADVERUM BIOTECHNOLOGIES, INC.
Reel/Frame 039113/0225 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Apr 29, 2015
From: CHALBERG, THOMAS W., JR
To: AVALANCHE BIOTECHNOLOGIES, INC.
Reel/Frame 035527/0445 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Apr 29, 2015
From: PALANKER, DANIEL V.
To: THE BOARD OF TRUSTEES OF THE LELAND STANDFORD JUNIOR UNIVERSITY
Reel/Frame 035527/0449 →