IP Library Patent Application 14700529
Patent Application
App. No. 14/700,529

3' TARGETING OLIGONUCLEOTIDES FOR MODULATING RNA

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Quick Facts
Patent No.
US None
App. No.
14/700,529
Abstract

Aspects of the invention relate to methods for increasing gene expression in a targeted manner. In some embodiments, methods and compositions are provided that are useful for posttranscriptionally altering protein and/or RNA levels in a targeted manner. Aspects of the invention disclosed herein provide methods and compositions that are useful for protecting RNAs from degradation (e.g., exonuclease mediated degradation).

Claims (19)

1 - 90 . (canceled)

92 . An oligonucleotide comprising the general formula 5′-X 1 —X 2 -3′, wherein

X 1 comprises 2 to 20 pyrimidine nucleotides that form base pairs with adenine; and X 2 comprises a region of complementarity that is complementary with at least 3 contiguous nucleotides of a poly-adenylated RNA transcript, wherein the nucleotide at the 5′-end of the region of complementary of X 2 is complementary with the nucleotide of the RNA transcript that is immediately internal to the poly-adenylation junction of the RNA transcript.

93 . The oligonucleotide of claim 92 , wherein X 1 comprises 2 to 20 thymidines or uridines.

94 . The oligonucleotide of claim 92 , wherein the oligonucleotide comprises at least one modified internucleoside linkage.

95 . The oligonucleotide of claim 92 , wherein the oligonucleotide comprises at least one modified nucleotide.

96 . The oligonucleotide of claim 92 , wherein at least one nucleotide of the oligonucleotide comprises a 2′ O-methyl.

97 . The oligonucleotide of claim 92 , wherein the oligonucleotide comprises at least one ribonucleotide, at least one deoxyribonucleotide, at least one 2′-fluoro-deoxyribonucleotides or at least one bridged nucleotide.

98 . The oligonucleotide of claim 97 , wherein the bridged nucleotide is a LNA nucleotide, a cEt nucleotide or a ENA modified nucleotide.

99 . The oligonucleotide of claim 92 , wherein each nucleotide of the oligonucleotide is a LNA nucleotide.

100 . The oligonucleotide of claim 92 , wherein the nucleotides of the oligonucleotide comprise alternating deoxyribonucleotides and 2′-fluoro-deoxyribonucleotides, 2′-O-methyl nucleotides, or bridged nucleotides.

101 . The oligonucleotide of claim 92 , wherein the oligonucleotide is a mixmer.

102 - 108 . (canceled)

109 . A composition comprising a plurality of oligonucleotides, wherein each of at least 75% of the oligonucleotides is an oligonucleotide of claim 92 .

110 - 114 . (canceled)

118 . A pharmaceutical composition comprising an oligonucleotide of claim 92 and a pharmaceutically acceptable carrier.

119 - 142 . (canceled)

143 . The oligonucleotide of claim 92 , wherein the RNA transcript is an mRNA, non-coding RNA, long non-coding RNA, miRNA, snoRNA, tRNAs, snRNAs, extracellular RNAs.

144 - 155 . (canceled)

Assignments (1)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded May 29, 2015
From: OZSOLAK, FATIH
To: RANA THERAPEUTICS, INC.
Reel/Frame 035744/0395 →