IP Library Granted Patent US 10,765,760
Granted Patent B2
US 10,765,760 · App. 15/993,287 · Granted Sep 8, 2020

Exon skipping oligomer conjugates for muscular dystrophy

Inventors: Gunnar J. Hanson (Cambridge, MA); Marco A. Passini (Cambridge, MA); Frederick Joseph Schnell (Cambridge, MA)
Assignee: Sarepta Therapeutics, Inc.
A61K47/6807A61K9/0019C07K14/4707C12N15/113C12N15/62
View Patent ↗
Loading inventors, assignments & file history…
Monitor This Case
Get email alerts when status or documents change.
Order Certified Copies
Most orders are placed with the USPTO same day — all within 24 business hours.
Order via The Patent Place →
Pre-filled with this patent's details
Quick Facts
Patent No.
US 10,765,760
App. No.
15/993,287
Granted
Sep 8, 2020
Kind
B2
Abstract

Antisense oligomer conjugates complementary to a selected target site in the human dystrophin gene to induce exon 52 skipping are described.

Claims (5)

1. An antisense oligomer conjugate of Formula (IV):

or a pharmaceutically acceptable salt thereof.

2. The antisense oligomer conjugate of claim 1 , wherein the antisense oligomer is of Formula (IVA):

3. A pharmaceutical composition, comprising an antisense oligomer conjugate of claim 1 , or a pharmaceutically acceptable salt thereof, and a pharmaceutically acceptable carrier.

4. A pharmaceutical composition, comprising an antisense oligomer conjugate of claim 2 , or a pharmaceutically acceptable salt thereof, and a pharmaceutically acceptable carrier.

Assignments (2)
SECURITY INTEREST Recorded May 7, 2025
From: SAREPTA THERAPEUTICS, INC.
To: JPMORGAN CHASE BANK, N.A. AS ADMINISTRATIVE AGENT
Reel/Frame 071218/0445 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Aug 5, 2022
From: HANSON, GUNNAR J.; PASSINI, MARCO A.; SCHNELL, FREDERICK JOSEPH
To: SAREPTA THERAPEUTICS, INC.
Reel/Frame 060737/0238 →