Patent Application
App. No. 16/434,799
COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
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Abstract
Improved compositions and methods for treating muscular dystrophy by administering antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping are described.
Claims (1)
1 . A method for treating Duchenne muscular dystrophy in a patient in need thereof comprising administering to the patient a dose of eteplirsen of about 30 mg/kg once a week.
Assignments (3)
RELEASE OF SECURITY INTEREST
Recorded Sep 16, 2022
From: BIOPHARMA CREDIT PLC
To: SAREPTA THERAPEUTICS, INC.
Reel/Frame 061120/0886 →
CORRECTIVE ASSIGNMENT TO CORRECT THE TYPOGRAPHICAL ERROR APP. NO 62/869,456 SHOULD BE CORRECTED AS 62/863,456 PREVIOUSLY RECORDED AT REEL: 051355 FRAME: 0280. ASSIGNOR(S) HEREBY CONFIRMS THE ASSIGNMENT.
Recorded Jan 9, 2020
From: SAREPTA THERAPEUTICS, INC.
To: BIOPHARMA CREDIT PLC
Reel/Frame 051554/0339 →
SECURITY INTEREST
Recorded Dec 23, 2019
From: SAREPTA THERAPEUTICS, INC.
To: BIOPHARMA CREDIT PLC
Reel/Frame 051355/0280 →