IP Library › Patent Application 17506846
Patent Application
App. No. 17/506,846

COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

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Quick Facts
Patent No.
US None
App. No.
17/506,846
Abstract

Improved compositions and methods for treating muscular dystrophy by administering antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping are described.

Claims (4)

1 - 23 . (canceled)

24 . An antisense oligonucleotide of 23 nucleotides in length, comprising the nucleotide sequence of SEQ ID NO: 112, wherein the uracil bases are optionally thymine bases.

25 . The antisense oligonucleotide of claim 24 , wherein the antisense oligonucleotide is a phosphorodiamidate morpholino oligomer.

26 . The antisense oligonucleotide of claim 24 or 25 , wherein the antisense oligonucleotide is chemically linked to a polyethylene glycol chain.