IP Library › Patent Application 17567252
Patent Application
App. No. 17/567,252

COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

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Quick Facts
Patent No.
US None
App. No.
17/567,252
Abstract

Improved compositions and methods for treating muscular dystrophy by administering antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping are described.

Claims (1)

1 . A method for treating Duchenne muscular dystrophy in a patient in need thereof comprising administering to the patient a dose of eteplirsen of about 30 mg/kg once a week.