IP Library Granted Patent US 12,459,941
Granted Patent B2
US 12,459,941 · App. 18/192,813 · Granted Nov 4, 2025

Tricyclic IRAK inhibitors

Inventors: Zhushou Luo (South San Francisco, CA); Simon Shaw (South San Francisco, CA); Ihab Darwish (South San Francisco, CA); Esteban Masuda (South San Francisco, CA); Chrystelle Lamagna (South San Francisco, CA)
Assignee: Rigel Pharmaceuticals, Inc.
C07D471/04C07F7/0812
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Quick Facts
Patent No.
US 12,459,941
App. No.
18/192,813
Granted
Nov 4, 2025
Kind
B2
Abstract

Disclosed embodiments concern compounds according to Formula I In some embodiments, the compounds are useful as kinase inhibitors, such as interleukin receptor associated kinases (IRAK) inhibitors. Also disclosed are compositions comprising such inhibitors, and methods of making and using the compounds and compositions. The disclosed compounds and/or compositions may be used to treat or prevent a kinase-associated disease or condition, particularly an IRAK-associated disease or condition.

Claims (88)

1. A compound according to Formula I

or a pharmaceutically acceptable salt or solvate thereof,

wherein:

Y is O(CH 2 ) n ;

n is 1, or 2;

Z 1 is N;

Z 2 and Z 3 are CR 5 ;

R 1 is H, halo, cyano, —SO 2 alkyl, N 3 , Si(C 1-6 alkyl) 3 , heterocycloalkyl, heteroaryl, or R a ;

R 2 is pyrrolidi-2-one, optionally substituted with a halogen and/or C 1 -C 4 alkyl;

R 3 is H or R a ;

each R 5 is H;

each R a is independently selected from C 1-6 alkyl, C 2-6 alkenyl, C 2-6 alkynyl, C 1-6 haloalkyl, aralkyl, or C 3-8 cycloalkyl, and may be optionally substituted with 1, 2, or 3 R b ;

each R b is independently selected from OH, —OR a , halo, oxo, —NR c R c , —C(O)OR d , —C(O)NR c R c , —N(R d )C(O)OR a , or —N(R d )C(O)NR c R c ;

each R c is independently selected from R d or two R c , together, with the nitrogen atom to which they are attached, form a C 2-8 heterocyclyl optionally having one or two additional heteroatoms selected from O and NR d and optionally substituted with one or more of the same or different R a or R b , and

each R d is independently selected from hydrogen and C 1-6 alkyl.

2. The compound or a pharmaceutically acceptable salt or solvate thereof of claim 1 , wherein the compound has a structure according to Formula II

3. The compound of claim 1 , wherein:

R 1 is R a ;

R 3 is H;

each R 5 is H;

or a combination thereof.

4. The compound of claim 1 , wherein R 1 is C 1-6 alkyl optionally substituted with 1, 2 or 3 R b .

5. The compound of claim 1 , wherein Y is —OCH 2 —.

6. The compound or a pharmaceutically acceptable salt or solvate thereof of claim 1 , wherein the compound has a structure according to Formula III

7. The compound of claim 1 , wherein:

R 2 is

m is 0, 1, 2 or 3; and

each R 6 independently is R a or R b .

8. The compound of claim 1 , wherein:

R 2 is

 and

each of R 7 and R 8 independently is halo or C 1-6 alkyl.

9. The compound of claim 8 , wherein the compound has a structure selected from Formulas IV-B, IV-C, or IV-D

10. The compound or a pharmaceutically acceptable salt or solvate thereof of claim 1 , selected from:

I-1: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)-4-(thiazol-5-yl)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-2: (S)-4-methyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one formic acid salt;

I-3: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)-4-(pyridin-3-yl)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-4:4-cyclopropyl-6-(((2S,3S,4S)-3-ethyl-4-fluoro-5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-5: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-6: (S)-4-iodo-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-7: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)-4-vinylpyrido [3,4-g]isoquinolin-1(2H)-one;

I-8: (S)-4-ethyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-9: (S)-4-allyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-10: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)-4-propylpyrido [3,4-g]isoquinolin-1(2H)-one;

I-11: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)-4-(prop-1-en-2-yl)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-12: (S)-4-cyclobutyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-13: (S)-4-cyclopentyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-14: (S)-4-cyclopropyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-15: (S)-4-isopropyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-16: (S)-1-oxo-6-((5-oxopyrrolidin-2-yl)methoxy)-1,2-dihydropyrido [3,4-g]isoquinoline-4-carbonitrile;

I-17: (S)-4-(2,2-difluoroethyl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-18: (S)-4-ethynyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-19: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)-4-(2,2,2-trifluoroethyl)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-20: (S)-4-(2-hydroxypropan-2-yl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-21: (S)-4-(3-hydroxyprop-1-yn-1-yl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-22: (S)-4-(2-hydroxyethyl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-23: (S)-4-(azetidin-3-yl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-24: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)-4-(prop-1-yn-1-yl)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-25: (S)-4-methyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-26: (S)-4-(2-aminopropan-2-yl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-27: (S)-1-oxo-6-((5-oxopyrrolidin-2-yl)methoxy)-1,2-dihydropyrido [3,4-g]isoquinoline-4-carboxamide;

I-28: (S)-4-acetyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-29: (S)-4-(3-aminoprop-1-yn-1-yl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-30: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)-4-(trifluoromethyl)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-31: (S,Z)-4-(2-ethoxyvinyl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-32: (S)-4-(1-ethoxyvinyl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-33: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)-4-(1H-pyrazol-4-yl)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-34: (S)-2-(1-oxo-6-((5-oxopyrrolidin-2-yl)methoxy)-1,2-dihydropyrido[3,4-g]isoquinolin-4-yl)acetaldehyde;

I-36:4-(1-hydroxyethyl)-6-(((S)-5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-37:4-(2-hydroxybut-3-yn-2-yl)-6-(((S)-5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-38: tert-butyl(S)-3-(1-oxo-6-((5-oxopyrrolidin-2-yl)methoxy)-1,2-dihydropyrido[3,4-g]isoquinolin-4-yl) azetidine-1-carboxylate;

I-39: tert-butyl(S)-2-(1-oxo-6-((5-oxopyrrolidin-2-yl)methoxy)-1,2-dihydropyrido[3,4-g]isoquinolin-4-yl)acetate;

I-40: (S)-2-(1-oxo-6-((5-oxopyrrolidin-2-yl)methoxy)-1,2-dihydropyrido[3,4-g]isoquinolin-4-yl)acetic acid;

I-41: (S)-2-(1-oxo-6-((5-oxopyrrolidin-2-yl)methoxy)-1,2-dihydropyrido[3,4-g]isoquinolin-4-yl)acetamide;

I-42: tert-butyl(S)-(3-(1-oxo-6-((5-oxopyrrolidin-2-yl)methoxy)-1,2-dihydropyrido[3,4-g]isoquinolin-4-yl) prop-2-yn-1-yl)carbamate;

I-44: 6-(((2S,3S,4S)-3-ethyl-4-fluoro-5-oxopyrrolidin-2-yl)methoxy)-4-iodopyrido[3,4-g]isoquinolin-1(2H)-one;

I-45: 6-(((2S,3S,4S)-3-ethyl-4-fluoro-5-oxopyrrolidin-2-yl)methoxy)-4-methylpyrido[3,4-g]isoquinolin-1(2H)-one;

I-46: 6-(((2S,3S,4S)-3-ethyl-4-fluoro-5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-47: 6-(((2S,3S,4S)-3-ethyl-4-fluoro-5-oxopyrrolidin-2-yl)methoxy)-1-oxo-1,2-dihydropyrido[3,4-g]isoquinoline-4-carbonitrile; or

I-48: (S)-4-(methylsulfonyl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-49: (S)-4-(3-hydroxy-3-methylbut-1-yn-1-yl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one;

I-50: (S)-4-isobutyl-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one; and

I-51: 6-(((2S,3S,4S)-3-ethyl-4-fluoro-5-oxopyrrolidin-2-yl)methoxy)-4-isopropylpyrido[3,4-g]isoquinolin-1(2H)-one.

11. The compound of claim 1 , wherein the compound is in the form of a pharmaceutically acceptable salt.

12. A pharmaceutical composition, comprising the compound or a pharmaceutically acceptable salt or solvate thereof of claim 1 and a pharmaceutically acceptable excipient.

13. A compound selected from:

I-35: (S)-4-(2-azidopropan-2-yl)-6-((5-oxopyrrolidin-2-yl)methoxy)pyrido[3,4-g]isoquinolin-1(2H)-one and

I-43: (S)-6-((5-oxopyrrolidin-2-yl)methoxy)-4-((triisopropylsilyl)ethynyl)pyrido[3,4-g]isoquinolin-1(2H)-one.

Assignments (2)
SECURITY INTEREST Recorded May 8, 2026
From: RIGEL PHARMACEUTICALS, INC.
To: MIDCAP FUNDING IV TRUST
Reel/Frame 075576/0880 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded May 11, 2023
From: LUO, ZHUSHOU; SHAW, SIMON; DARWISH, IHAB; MASUDA, ESTEBAN; LAMAGNA, CHRYSTELLE
To: RIGEL PHARMACEUTICALS, INC.
Reel/Frame 063610/0214 →
Continuity (2)
Provisional Application 63325957 · Mar 31, 2022
Related Publication 20230312568A1 · Oct 5, 2023
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