IP Library Granted Patent US 7,825,267
Granted Patent B2
US 7,825,267 · App. 11/852,278 · Granted Nov 2, 2010

Synthesis of FR901464 and analogs with antitumor activity

Assignee: University of Pittsburgh-of the Commonwealth System of Higher Education
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Quick Facts
Patent No.
US 7,825,267
App. No.
11/852,278
Granted
Nov 2, 2010
Kind
B2
Abstract

The present invention provides novel analogs of FR901464, as well as an improved methodology for preparing FR901464 and its analogs. These compounds display an anti-cancer activity and are candidates for therapies against a number of disease states associated with dysfunctional RNA splicing.

Claims (89)

1. A compound, stereoisomer, or pharmaceutically acceptable salt or ester thereof having Formula I:

wherein

R 1 and R 8 are independently selected from the group consisting of H, C 1-6 -alkyl, halo(C 1-6 -alkyl), C(O)R 11 , C(O)OR 11 , and C(O)NR 12 R 13 ,

wherein each R 11 is independently H, C 1-6 -alkyl, or halo(C 1-6 -alkyl), and

wherein R 12 and R 13 are selected independently from the group consisting of H, C 1-6 -alkyl, and halo(C 1-6 -alkyl);

or R 12 and R 13 , together with the nitrogen atom to which they are bound, form a heterocyclic or heterocyclic ring;

R 2 , R 3 , R 4 , R 5 , and R 6 are independently selected from the group consisting of H, C 1-6 -alkyl, and halo(C 1-6 -alkyl);

R 7 is selected from the group consisting of H, C 1-6 -alkyl and halo(C 1-6 -alkyl); and

R 9 and R 10 are independently selected from the group consisting of H, OH, C 1-6 -alkyl, and C 1-6 -alkyl substituted with one to three groups independently selected from halo, hydroxy, and C 1-6 -alkoxy;

R 14 and R 15 are selected independently from the group consisting of halo(C 1-6 -alkyl), C(O)R 11 , F, Cl, NO 2 , and B(OR 11 ) 2 , wherein R 11 is as defined above;

or R 14 and R 15 , together with the carbon atom to which they are bound, form an epoxide ring;

provided that when R 1 is C(O)CH 3 , R 2 , R 4 , and R 8 are hydrogen, and R 3 , R 5 , R 6 , R 7 , and R 9 are methyl, then R 10 is not hydrogen or OH.

2. The compound according to claim 1 having Formula Ib:

wherein R 1 , R 2 , R 3 , R 4 , R 5 , R 6 , R 7 , R 8 , R 9 , and R 10 are as defined in claim 1 .

3. The compound according to claim 2 wherein R 1 is C(O)R 11 and R 11 is C 1-6 -alkyl or halo(C 1-6 -alkyl).

4. The compound according to claim 3 wherein R 1 is C(O)CH 3 .

5. The compound according to claim 2 wherein at least one of R 2 , R 3 , R 5 , and R 6 is C 1-6 -alkyl.

6. The compound according to claim 5 wherein at least one of R 2 , R 3 , R 5 , and R 6 is CH 3 .

7. The compound according to claim 2 wherein R 4 is hydrogen.

8. The compound according to claim 2 wherein R 7 is CH 3 or CF 3 .

9. The compound according to claim 2 wherein at least one of R 9 and R 10 is independently selected from the group consisting of C 1-6 -alkyl and C 1-6 -alkyl substituted with one to three groups independently selected from halo, hydroxy, and C 1-6 -alkoxy.

10. The compound according to claim 9 wherein at least one of R 9 and R 10 is independently selected from the group consisting of CH 3 , CH 2 I, and CH 2 OH.

11. The compound according to claim 1 having Formula (Ic):

wherein R 1 , R 2 , R 3 , R 4 , R 5 , R 6 , R 7 , and R 8 are as defined in claim 1 .

12. The compound according to claim 11 wherein R 1 is C(O)R 11 and R 11 is C 1-6 -alkyl or halo(C 1-6 -alkyl).

13. The compound according to claim 12 wherein R 1 is C(O)CH 3 .

14. The compound according to claim 11 wherein at least one of R 2 , R 3 , R 5 , and R 6 is C 1-6 -alkyl.

15. The compound according to claim 14 wherein at least one of R 2 , R 3 , R 5 , and R 6 is CH 3 .

16. The compound according to claim 11 wherein R 4 is hydrogen.

17. The compound according to claim 11 wherein R 7 is CH 3 or CF 3 .

18. The compound according to claim 1 that is selected from the group consisting of:

19. The compound according to claim 18 or a stereoisomer or pharmaceutically acceptable salt or ester thereof of Formula (IX):

20. A pharmaceutical composition comprising a compound according to claim 1 , a stereoisomer, or pharmaceutically acceptable salt or ester thereof and a pharmaceutically acceptable carrier.

21. The composition according to claim 20 comprising a compound or pharmaceutically acceptable salt or ester thereof of Formula (IX):

22. A process for preparing a compound, stereoisomer, or pharmaceutically acceptable salt or ester thereof having Formula I:

wherein

R 1 and R 8 are independently selected from the group consisting of H, Pg, C 1-6 -alkyl, halo(C 1-6 -alkyl), C(O)R 11 , C(O)OR 11 , and C(O)NR 12 R 13 ,

wherein each R 11 is independently H, C 1-6 -alkyl, or halo(C 1-6 -alkyl), and

wherein R 12 and R 13 are selected independently from the group consisting of H, C 1-6 -alkyl, and halo(C 1-6 -alkyl);

or R 12 and R 13 , together with the nitrogen atom to which they are bound, form a 5- to 6-membered heterocyclic or heteroaromatic ring;

R 2 , R 3 , R 4 , R 5 , and R 6 are independently selected from the group consisting of H, C 1-6 -alkyl, and halo(C 1-6 -alkyl);

R 7 is selected from the group consisting of H, C 1-6 -alkyl and halo(C 1-6 -alkyl); and

R 9 and R 10 are independently selected from the group consisting of H, OH, C 1-6 -alkyl, and C 1-6 -alkyl substituted with one to three groups independently selected from halo, hydroxy, C 1-6 -alkoxy, and OPg;

R 14 and R 15 are selected independently from the group consisting of halo(C 1-6 -alkyl), C(O)R 11 , F, Cl, NO 2 , and B(OR 11 ) 2 , wherein R 11 is as defined above;

or R 14 and R 15 , together with the carbon atom to which they are bound, form an epoxide ring; and

each Pg is independently a hydroxy protecting group;

said method comprising contacting a compound of Formula (II) wherein E, R 1 , R 2 , R 3 , R 4 , R 5 , R 6 , and R 7 are as defined above:

with a compound of Formula (III) wherein R 8 , R 9 , R 10 , R 14 , and R 15 are as defined above:

in the presence of an olefin metathesis catalyst to provide a compound of Formula I

provided that when R 1 is C(O)CH 3 ; R 2 , R 4 , and R 8 are hydrogen; R 3 , R 5 , R 6 , R 7 , and R 9 are methyl; and R 10 is OH, then the compound of Formula (III) is a compound of Formula (IIIa):

23. The process according to claim 22 , wherein the compound of Formula I is compound (IX):

24. A process for preparing compound, stereoisomer, or pharmaceutically acceptable salt or ester thereof having Formula I:

wherein

R 1 and R 8 are independently selected from the group consisting of H, Pg, C 1-6 -alkyl, halo(C 1-6 -alkyl), C(O)R 11 , C(O)OR 11 , and C(O)NR 12 R 13 ,

wherein each R 11 is independently H, C 1-6 -alkyl, or halo(C 1-6 -alkyl), and

wherein R 12 and R 13 are selected independently from the group consisting of H, C 1-6 -alkyl, and halo(C 1-6 -alkyl);

or R 12 and R 13 , together with the nitrogen atom to which they are bound, form a 5- to 6-membered heterocyclic or heteroaromatic ring;

R 2 , R 3 , R 4 , R 5 , and R 6 are independently selected from the group consisting of H, C 1-6 -alkyl, and halo(C 1-6 -alkyl);

R 7 is selected from the group consisting of H, C 1-6 -alkyl and halo(C 1-6 -alkyl); and

R 9 and R 10 are independently selected from the group consisting of H, OH, C 1-6 -alkyl, and C 1-6 -alkyl substituted with one to three groups independently selected from halo, hydroxy, C 1-6 -alkoxy, and OPg;

R 14 and R 15 are selected independently from the group consisting of halo(C 1-6 -alkyl), C(O)R 11 , F, Cl, NO 2 , and B(OR 11 ) 2 , wherein R 11 is as defined above;

or R 14 and R 15 , together with the carbon atom to which they are bound, form an epoxide ring;

said process comprising:

(a) contacting a compound of Formula (IVc), wherein R 9 , R 14 , and R 15 are as defined above and P 1 is a hydroxy protecting group, with an oxidizing agent to form a first compound of Formula (V) wherein R 9 , R 14 , and R 15 are as defined above, P 1 is a hydroxy protecting group, and P 2 is hydrogen:

(b) converting said first compound of Formula (V) wherein P 1 is a hydroxy protecting group and P 2 is hydrogen to a second compound of Formula (V) wherein P 1 and P 2 are hydroxy protecting groups;

(c) optionally converting said first or second compound of Formula (V) under cyclization conditions to a compound of Formula (III) wherein R 8 , R 9 , and R 10 are as defined herein:

(d) optionally converting said second compound of Formula (V) under oxidative conditions to a compound of Formula (VI) wherein R 9 , R 14 , and R 15 are as defined above, and P 1 and P 2 are hydroxy protecting groups; and converting the compound of Formula (VI) under cyclization conditions to a compound of Formula (III):

(e) contacting a compound of Formula (III) with a compound of Formula (II) wherein R 1 , R 2 , R 3 , R 4 , R 5 , R 6 , and R 7 are as defined herein:

in the presence of an olefin metathesis catalyst to form a compound of Formula I.

25. The process according to claim 24 , said process further comprising:

(a) contacting a compound of Formula (VII) with Ag—CC—CO 2 Me and Cp 2 ZrCl 2 to form a compound of Formula (VIII) wherein R 9 , R 14 , and R 15 are as defined in claim 24 :

(b) contacting a compound of Formula (VIII) with Red-Al to form a compound of Formula (IVa) wherein P 1 is hydrogen:

(c) converting a compound of Formula (IVa) wherein P 1 is hydrogen to a compound of Formula (IVa) wherein P 1 is a hydrogen protecting group;

(d) contacting a compound of Formula (IVa) wherein P 1 is a hydrogen protecting group with a reducing agent to form a compound of Formula (IVb) wherein P 1 is a hydrogen protecting group

(e) reacting a compound of Formula (IVb) wherein P 1 is a hydrogen protecting group with o-O 2 N-PhSeCN under selenide forming conditions to a compound of Formula (IVc:

26. The process according to claim 24 , wherein the compound of Formula I is compound (X):

27. The process according to claim 24 , wherein the compound of Formula I is compound (IX):

28. An intermediate compound having Formula (IV):

wherein

Y is selected from the group consisting of MeO 2 C—, o-O 2 N-PhSeCH 2 —, and HOCH 2 —;

R 9 is selected from the group consisting of C 1-6 -alkyl and C 1-6 -alkyl substituted with one to three groups independently selected from halo, hydroxy, C 1-6 -alkoxy, and OPg;

R 14 and R 15 are selected independently from the group consisting of halo(C 1-6 -alkyl), C(O)R 11 , F, Cl, NO 2 , and B(OR 11 2 , wherein each R 11 is independently H, C 1-6 -alkyl, or halo(C 1-6 -alkyl),

or R 14 and R 15 , together with the carbon atom to which they are bound, form an epoxide ring; and

P 1 and Pg are independently a hydroxy protecting group.

29. The intermediate compound according to claim 28 wherein P 1 is triethylsilyl and R 9 is C 1-6 -alkyl.

30. The intermediate compound according to claim 29 that is selected from the group consisting of:

31. The composition according to claim 20 comprising a compound or pharmaceutically acceptable salt of ester thereof of:

32. The process according to claim 22 , wherein the compound of Formula I is

33. The process according to claim 24 , wherein the compound of Formula I is

Assignments (2)
CONFIRMATORY LICENSE Recorded Feb 24, 2010
From: UNIVERSITY OF PITTSBURGH
To: NATIONAL INSTITUTES OF HEALTH (NIH), U.S. DEPT. OF HEALTH AND HUMAN SERVICES (DHHS), U.S. GOVERNMENT
Reel/Frame 023980/0769 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Jan 11, 2008
From: KOIDE, KAZUNORI; ALBERT, BRIAN J.; SIVARAMAKRISHNAN, ANANTHAPADMANABHAN
To: UNIVERSITY OF PITTSBURGH -- OF THE COMMONWEALTH SYSTEM OF HIGHER EDUCATION
Reel/Frame 020356/0056 →
Continuity (3)
Provisional Application 6084323000 · Sep 8, 2006
Provisional Application 6095232600 · Jul 27, 2007
Related Publication 20080096879A1 · Apr 24, 2008