IP Library Granted Patent US 9,745,610
Granted Patent B2
US 9,745,610 · App. 14/248,980 · Granted Aug 29, 2017

Methods and compositions for controlling gene expression by RNA processing

Inventors: Jennifer A. Doudna (Berkeley, CA); Lei S. Qi (El Cerrito, CA); Rachel E. Haurwitz (Kensington, CA); Adam P. Arkin (San Francisco, CA)
Assignee: The Regents of the University of California
C12P19/34C12N15/85C12N2830/50
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Quick Facts
Patent No.
US 9,745,610
App. No.
14/248,980
Granted
Aug 29, 2017
Kind
B2
Abstract

The present disclosure provides nucleic acids encoding an RNA recognition sequence positioned proximal to an insertion site for the insertion of a sequence of interest; and host cells genetically modified with the nucleic acids. The present disclosure also provides methods of modifying the activity of a target RNA, and kits and compositions for carrying out the methods.

Claims (25)

1. A recombinant expression vector comprising:

a first recognition nucleotide sequence that encodes an RNA recognition sequence recognized by a Csy4 endoribonuclease, wherein the first recognition nucleotide sequence is positioned between a first coding region and a first regulatory element positioned 5′ of the coding region; and

a second recognition nucleotide sequence that encodes an RNA recognition sequence recognized by the Csy4 endoribonuclease, wherein the second recognition nucleotide sequence is positioned between the first coding region and a second coding region positioned 3′ of the first coding region,

wherein the Csy4 endoribonuclease is enzymatically active and comprises an amino acid sequence having at least about 75% amino acid sequence identity to the amino acid sequence set forth in one of SEQ ID NOs: 1-55, 132-133, and 147-149.

2. The recombinant expression vector of claim 1 , wherein less than 50 nucleotides are disposed between the recognition nucleotide sequence and the insertion site.

3. The recombinant expression vector of claim 1 , further comprising a promoter 5′ of the recognition nucleotide sequence, wherein the promoter is operably linked to the recognition nucleotide sequence and to the insertion site.

4. The recombinant expression vector of claim 1 , further comprising a nucleotide sequence encoding the Csy4 endoribonuclease.

5. The recombinant expression vector of claim 1 , wherein the Csy4 endoribonuclease comprises an amino acid sequence having at least about 95% amino acid sequence identity to the amino acid sequence set forth in one of SEQ ID NOs: 1-55, 132-133, and 147-149.

6. The recombinant expression vector of claim 1 , wherein the RNA recognition sequence is at least about 90% identical to the RNA recognition sequence set forth in one of SEQ ID NOs: 56-131.

7. A genetically modified cell comprising the recombinant expression vector of claim 1 .

8. The genetically modified cell of claim 7 , further comprising a second recombinant expression vector encoding the Csy4 endoribonuclease.

9. The genetically modified cell of claim 7 , wherein the cell is selected from a group consisting of an archaeal cell, a bacterial cell, and a eukaryotic cell.

10. The genetically modified cell of claim 7 , wherein the cell is a mammalian cell.

11. The genetically modified cell of claim 7 , wherein the cell is selected from a group consisting of a eukaryotic single-cell organism, a somatic cell, a germ cell, and a stem cell.

12. A composition for modifying the activity of a target RNA, the composition comprising:

(i) a recombinant target RNA comprising:

a first RNA recognition sequence that is recognized by a Csy4 endoribonuclease and is positioned between a first coding region and a first regulatory element 5′ of the coding region; and,

a second RNA recognition sequence that is recognized by the Csy4 endoribonuclease and is positioned between the first coding region and a second coding region positioned 3′ of the first coding region; and

(ii) an enzymatically active Csy4 endoribonuclease.

13. The composition of claim 12 , wherein the Csy4 endoribonuclease comprises an amino acid sequence having at least about 75% amino acid sequence identity to the amino acid sequence set forth in one of SEQ ID NOs: 1-55, 132-133, and 147-149.

14. The composition of claim 12 , wherein the RNA recognition sequence is at least about 90% identical to the RNA recognition sequence set forth in one of SEQ ID NOs: 56-131.

15. The composition of claim 12 , wherein the Csy4 endoribonuclease comprises an amino acid sequence having at least about 95% amino acid sequence identity to the amino acid sequence set forth in one of SEQ ID NOs: 1-55, 132-133, and 147-149.

16. The recombinant expression vector of claim 1 , further comprising a third recognition nucleotide sequence that encodes an RNA recognition sequence recognized by the Csy4 endoribonuclease, wherein the third recognition nucleotide sequence is positioned between the second coding region and a second regulatory sequence positioned 3′ of the second coding region.

17. The composition of claim 12 , further comprising a third RNA recognition sequence that is recognized by the Csy4 endoribonuclease and is positioned (c) between the second coding region and a second regulatory sequence positioned 3′ of the second coding region.

18. The composition of claim 12 , wherein the Csy4 endoribonuclease comprises an amino acid sequence having at least about 85% amino acid sequence identity to the amino acid sequence set forth in one of SEQ ID NOs: 1-55, 132-133, and 147-149.

Assignments (3)
CONFIRMATORY LICENSE Recorded Jan 15, 2016
From: REGENTS OF THE UNIVERSITY OF CALIFORNIA, THE
To: ENERGY, UNITED STATES DEPARTMENT OF
Reel/Frame 037565/0148 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Aug 28, 2015
From: DOUDNA, JENNIFER A.; QI, LEI S.; HAURWITZ, RACHEL E.; ARKIN, ADAM P.
To: THE REGENTS OF THE UNIVERSITY OF CALIFORNIA
Reel/Frame 036453/0196 →
CONFIRMATORY LICENSE Recorded Dec 30, 2014
From: UNIVERSITY OF CALIFORNIA BERKELEY
To: NATIONAL SCIENCE FOUNDATION
Reel/Frame 034714/0332 →
Continuity (3)
Continuation PCTUS2013053287 · Aug 1, 2013
Provisional Application 61679397 · Aug 3, 2012
Related Publication 20140302563A1 · Oct 9, 2014