IP Library › Granted Patent US 10,780,131
Granted Patent B2
US 10,780,131 · App. 16/144,786 · Granted Sep 22, 2020

Ameliorating nervous systems disorders

Inventors: Arnold Kriegstein (Mill Valley, CA); John L. R. Rubenstein (San Francisco, CA); Scott C. Baraban (Novato, CA); Arturo Alvarez-Buylla (Woodside, CA)
Assignee: The Regents of the University of California
A61K35/30A61K9/0019A61K9/0085C12N5/0618C12N5/0622C12N2506/02G01N2800/28G01N2800/2835G01N2800/2842
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Quick Facts
Patent No.
US 10,780,131
App. No.
16/144,786
Granted
Sep 22, 2020
Kind
B2
Abstract

The present disclosure provides methods for the treatment of a mammal having a neurological condition, disease, or injury. The methods involve increasing the number of functional GABAergic interneurons at or near the site of the neurological disease, injury, or condition.

Claims (27)

1. A method for improving motor activity in the nervous system of a mammal having impaired motor activity, comprising:

transplanting genetically-modified medial ganglionic eminence (MGE) precursor cells into the nervous system of the mammal;

wherein the MGE precursor cells are genetically modified to allow tracking of the MGE precursor cells following transplantation.

2. The method of claim 1 , wherein the mammal has a central nervous system (CNS) disorder.

3. The method of claim 2 , wherein the genetically-modified MGE precursor cells are transplanted in or near the striatum.

4. The method of claim 2 , wherein the genetically-modified MGE precursor cells are transplanted in or near the neocortex.

5. The method of claim 1 , further comprising assessing the mammal for an improvement in motor activity following transplantation of the genetically-modified MGE precursor cells.

6. The method of claim 1 , wherein the MGE precursor cells are genetically modified to express a fluorescent protein.

7. The method of claim 6 , wherein the MGE precursor cells are genetically modified to express green fluorescent protein.

8. A method for improving motor activity in the nervous system of a mammal having impaired motor activity, comprising:

transplanting genetically-modified medial ganglionic eminence (MGE) precursor cells into the nervous system of the mammal;

wherein the MGE precursor cells are genetically modified to express an exogenous protein.

9. The method of claim 8 , wherein the exogenous protein is a neurotransmitter producing enzyme, a neurotrophin, a neural promoting growth factor, a neural inhibitory growth factor, or a neuropoietic cytokine.

10. The method of claim 8 , wherein the exogenous protein is a telomerase.

11. The method of claim 8 , wherein the genetically-modified MGE precursor cells differentiate into GAB Aergic neurons following transplantation, and where differentiation of the genetically-modified MGE precursor cells into GAB Aergic neurons is assessed by improvement in motor activity following transplantation of the genetically-modified MGE precursor cells.

12. The method of claim 8 , wherein the mammal has a central nervous system (CNS) disorder.

13. The method of claim 8 , wherein the genetically-modified MGE precursor cells are transplanted in or near the striatum.

14. The method of claim 8 , wherein the genetically-modified MGE precursor cells are transplanted in or near the neocortex.

15. A method for improving motor activity in the nervous system of a mammal having impaired motor activity, comprising:

transplanting genetically-modified medial ganglionic eminence (MGE) precursor cells into the nervous system of the mammal;

wherein the MGE precursor cells are genetically modified to modulate expression of a protein associated with neural function, wherein the protein is a neurotransmitter producing enzyme, a neurotrophin, a neural promoting growth factor, a neural inhibitory growth factor, a neuropoietic cytokine, or a telomerase.

16. The method of claim 15 , wherein the protein is a telomerase.

17. The method of claim 15 , wherein the genetically-modified MGE precursor cells differentiate into GAB Aergic neurons following transplantation, and where differentiation of the genetically-modified MGE precursor cells into GAB Aergic neurons is assessed by assaying motor activity following transplantation of the genetically-modified MGE precursor cells.

18. The method of claim 15 , wherein the mammal has a central nervous system (CNS) disorder.

19. The method of claim 18 , wherein the genetically-modified MGE precursor cells are transplanted in or near the striatum.

20. The method of claim 18 , wherein the genetically-modified MGE precursor cells are transplanted in or near the neocortex.

21. The method of claim 15 , wherein the protein is a neurotransmitter producing enzyme, a neurotrophin, a neural promoting growth factor, a neural inhibitory growth factor, or a neuropoietic cytokine.

Assignments (1)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Oct 29, 2018
From: KRIEGSTEIN, ARNOLD; RUBENSTEIN, JOHN L. R.; BARABAN, SCOTT C.; ALVAREZ-BUYLLA, ARTURO
To: THE REGENTS OF THE UNIVERSITY OF CALIFORNIA
Reel/Frame 047344/0328 →
Continuity (5)
Continuation 14943916 · Nov 17, 2015
Continuation 13744201 · Jan 17, 2013
Continuation 12991367
Provisional Application 61050980 · May 6, 2008
Related Publication 20190030084A1 · Jan 31, 2019