IP Library Granted Patent US 11,111,270
Granted Patent B2
US 11,111,270 · App. 16/740,240 · Granted Sep 7, 2021

Inhibitor of apoptosis protein (IAP) antagonists

Inventors: Nicholas David Peter Cosford (La Jolla, CA); Mitchell Dennis Vamos (La Jolla, CA)
Assignee: SANFORD BURNHAM PREBYS MEDICAL DISCOVERY INSTITUTE
C07K5/0806C07D487/04C07D487/14C07D498/04C07D498/10C07D513/04A61K38/00
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Quick Facts
Patent No.
US 11,111,270
App. No.
16/740,240
Filed
Jan 10, 2020
Granted
Sep 7, 2021
Kind
B2
Examiner
KIFLE, BRUCK
Art Unit
1624
USPC
514/413
Abstract

Provided herein are compounds that modulate the activity of inhibitor of apoptosis proteins (IAPs), compositions comprising the compounds, and methods of using the compounds and compositions comprising the compounds.

Claims (93)

1. A compound having the structure of Formula C-I, pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof:

wherein,

R 1 is H, C 1 -C 6 alkyl, C 3 -C 6 cycloalkyl, —C 1 -C 6 alkyl-(substituted or unsubstituted C 3 -C 6 cycloalkyl), substituted or unsubstituted aryl, substituted or unsubstituted heteroaryl, —C 1 -C 6 alkyl-(substituted or unsubstituted aryl), or —C 1 -C 6 alkyl-(substituted or unsubstituted heteroaryl);

X 1 is N—R A ;

X 2 is CR 2c R 2d ;

X 3 is CR 2a R 2b ;

R A is H, C 1 -C 6 alkyl, —C(═O)C 1 -C 6 alkyl, substituted or unsubstituted aryl, or substituted or unsubstituted heteroaryl;

W 1 is O, S, N—R a , or C(R 8a )(R 8b );

W 2 is O, S, N—R a , or C(R 8c )(R 8d ); provided that W 1 and W 2 are not both O, or both S;

R 2a , R 2b , R 2c , and R 2d are independently selected from H, substituted or unsubstituted C 1 -C 6 alkyl, substituted or unsubstituted C 3 -C 6 cycloalkyl, substituted or unsubstituted C 2 -C 5 heterocycloalkyl, substituted or unsubstituted aryl, substituted or unsubstituted heteroaryl, —C 1 -C 6 alkyl-(substituted or unsubstituted C 3 -C 6 cycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted C 2 -C 5 heterocycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted aryl), —C 1 -C 6 alkyl-(substituted or unsubstituted heteroaryl), and —C(═O)R B ;

R B is substituted or unsubstituted C 1 -C 6 alkyl, substituted or unsubstituted C 3 -C 6 cycloalkyl, substituted or unsubstituted C 2 -C 5 heterocycloalkyl, substituted or unsubstituted aryl, substituted or unsubstituted heteroaryl, —C 1 -C 6 alkyl-(substituted or unsubstituted C 3 -C 6 cycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted C 2 -C 5 heterocycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted aryl), —C 1 -C 6 alkyl-(substituted or unsubstituted heteroaryl), or —NR D R E ;

R D and R E are independently selected from H, substituted or unsubstituted C 1 -C 6 alkyl, substituted or unsubstituted C 3 -C 6 cycloalkyl, substituted or unsubstituted C 2 -C 5 heterocycloalkyl, substituted or unsubstituted aryl, substituted or unsubstituted heteroaryl, —C 1 -C 6 alkyl-(substituted or unsubstituted C 3 -C 6 cycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted C 2 -C 5 heterocycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted aryl), and —C 1 -C 6 alkyl-(substituted or unsubstituted heteroaryl);

m is 0, 1, or 2;

—U— is —NHC(═O)—, —C(═O)NH—, —NHS(═O) 2 —, —S(═O) 2 NH-, —NHC(═O)NH—, —NH(C═O)O-, —O(C═O)NH-, or —NHS(═O) 2 NH-;

R 3 is C 1 -C 3 alkyl or C 1 -C 3 fluoroalkyl;

R 4 is —NHR 5 , —N(R 5 ) 2 , —N + (R 5 ) 3 , or —OR 5 ;

each R 5 is independently selected from H, C 1 -C 3 alkyl, C 1 -C 3 haloalkyl, and —C 1 -C 3 alkyl-(C 3 -C 5 cycloalkyl);

or:

R 3 and R 5 together with the atoms to which they are attached form a substituted or unsubstituted 5-7 membered ring;

or:

R 3 is bonded to a nitrogen atom of U to form a substituted or unsubstituted 5-7 membered ring;

R 6 is —NHC(═O)R 7 , —C(═O)NHR 7 , —NHS(═O) 2 R 7 , —S(═O) 2 NHR 7 ; —NHC(═O)NHR 7 , —NHS(═O) 2 NHR 7 , -(C 1 -C 3 alkyl)-NHC(═O)R 7 , -(C 1 -C 3 alkyl)-C(═O)NHR 5 , -(C 1 -C 3 alkyl)-NHS(═O) 2 R 7 , -(C 1 -C 3 alkyl)-S(═O) 2 NHR 7 ; -(C 1 -C 3 alkyl)-NHC(═O)NHR 7 , -(C 1 -C 3 alkyl)-NHS(═O) 2 NHR 7 , substituted or unsubstituted C 2 -C 10 heterocycloalkyl, or substituted or unsubstituted heteroaryl;

each R 7 is independently selected from C 1 -C 6 alkyl, C 1 -C 6 haloalkyl, a substituted or unsubstituted C 3 -C 10 cycloalkyl, a substituted or unsubstituted C 2 -C 10 heterocycloalkyl, a substituted or unsubstituted aryl, a substituted or unsubstituted heteroaryl, —C 1 -C 6 alkyl-(substituted or unsubstituted C 3 -C 10 cycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted C 2 -C 10 heterocycloalkyl, —C 1 -C 6 alkyl-(substituted or unsubstituted aryl), —C 1 -C 6 alkyl-(substituted or unsubstituted heteroaryl), —(CH 2 ) P —CH(substituted or unsubstituted aryl) 2 , —(CH 2 ) P —CH(substituted or unsubstituted heteroaryl) 2 , —(CH 2 ) P —CH(substituted or unsubstituted aryl)(substituted or unsubstituted heteroaryl), -(substituted or unsubstituted aryl)-(substituted or unsubstituted aryl), -(substituted or unsubstituted aryl)-(substituted or unsubstituted heteroaryl), -(substituted or unsubstituted heteroaryl)-(substituted or unsubstituted aryl), and -(substituted or unsubstituted heteroaryl)-(substituted or unsubstituted heteroaryl);

p is 0, 1, or 2;

R 8a , R 8b , R 8c , and R 8d are independently selected from H, C 1 -C 6 alkyl, C 1 -C 6 fluoroalkyl, C 1 -C 6 alkoxy, and substituted or unsubstituted aryl;

or:

R 8a and R 8d are as defined above, and R 8b and R 8c together form a bond;

or:

R 8a and R 8d are as defined above, and R 8b and R 8c together with the atoms to which they are attached form a substituted or unsubstituted fused 5-7 membered saturated, or partially saturated carbocyclic ring or heterocyclic ring comprising 1-3 heteroatoms selected from S, O, and N, a substituted or unsubstituted fused 5-10 membered aryl ring, or a substituted or unsubstituted fused 5-10 membered heteroaryl ring comprising 1-3 heteroatoms selected from S, O, and N;

or:

R 8c and R 8d are as defined above, and R 8a and R 8b together with the atoms to which they are attached form a substituted or unsubstituted saturated, or partially saturated 3-7 membered spirocycle or heterospirocycle comprising 1-3 heteroatoms selected from S, O, and N;

or:

R 8a and R 8b are as defined above, and R 8c and R 8d together with the atoms to which they are attached form a substituted or unsubstituted saturated, or partially saturated 3-7 membered spirocycle or heterospirocycle comprising 1-3 heteroatoms selected from S, O, and N;

where each substituted alkyl, fused ring, spirocycle, cycloalkyl, heterocycloalkyl, aryl, or heteroaryl is substituted with 1-3 R 9 ;

each R 9 is independently selected from halogen, —OH, —SH, (C═O), CN, C 1 -C 4 alkyl, C 1 -C 4 fluoroalkyl, C 1 -C 4 alkoxy, C 1 -C 4 fluoroalkoxy, —NH 2 , —NH(C 1 -C 4 alkyl), —NH(C 1 -C 4 alkyl) 2 , —C(═O)OH, —C(═O)NH 2 , —C(═O)C 1 -C 3 alkyl, —S(═O) 2 CH 3 , —NH(C 1 -C 4 alkyl)-OH, —NH(C 1 -C 4 alkyl)-O—(C 1 -C 4 alkyl), —O(C 1 -C 4 alkyl)-NH 2 , —O(C 1 -C 4 alkyl)-NH—(C 1 -C 4 alkyl), and —O(C 1 -C 4 alkyl)-N—(C 1 -C 4 alkyl) 2 ; or two R 9 together with the atoms to which they are attached form a methylene dioxy or ethylene dioxy ring substituted or unsubstituted with halogen, —OH, or C 1 -C 3 alkyl;

where each heterocycloalkyl is independently selected from a monocyclic, fused bicyclic, and bridged bicyclic ring, where the heterocycloalkyl has from 2 to 10 carbons in the ring and heteroatoms selected from O, N, or S; and

where each heteroaryl is independently selected from a monocyclic and fused bicyclic ring, where the heteroaryl is a 5- to 14-membered ring system comprising one to thirteen carbon atoms, one to six heteroatoms selected from the group consisting of O, N, or S.

2. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, having the structure of Formula C-III-1:

wherein,

X 1 is N—R A ;

X 2 is CR 2c R 2d ; and

X 3 is CR 2a R 2b .

3. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, wherein,

X 1 is N—R a ;

X 2 is CR 2c R 2d ;

X 3 is CR 2a R 2b ;

—U— is —NHC(═O)— or —C(═O)NH—;

R 3 is C 1 -C 3 alkyl;

R 4 is —NHR 5 , —N(R 5 ) 2 , or —N + (R 5 ) 3 ; and

each R 5 is independently selected from H, C 1 -C 3 alkyl and —C 1 -C 3 alkyl-(C 3 -C 5 cycloalkyl).

4. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, wherein,

5. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, wherein,

6. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, wherein,

X 1 is N—R A ;

X 2 is CH 2 ; and

X 3 is CR 2a R 2b .

7. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, having the structure of Formula C-VIII-2:

8. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, having the structure of Formula C-XII:

wherein,

X 1 is N—R A ; and

X 2 is CR 2c R 2d .

9. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, wherein R 2a , R 2b R 2c , and R 2d , are independently H or C 1 -C 3 alkyl; and R 1 is H or methyl.

10. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, wherein R 1 is H.

11. The compound claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate or stereoisomer thereof, wherein R 6 is —C(═O)NHR 7 .

12. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate or stereoisomer thereof, wherein the compound of Formula C-I has the structure of C-XXI, or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof:

wherein,

W 2 is O, S, or C(R 8c )(R 8d );

R 1 is H or C 1 -C 6 alkyl;

X 1 is N—R A ;

R A is H, C 1 -C 6 alkyl, —C(═O)C 1 -C 6 alkyl, substituted or unsubstituted aryl, or substituted or unsubstituted heteroaryl;

R 2a and R 2b are independently selected from H, substituted or unsubstituted C 1 -C 6 alkyl, and —C(═O)R b ;

R B is substituted or unsubstituted C 1 -C 6 alkyl, —C 1 -C 6 alkyl-(substituted or unsubstituted C 3 -C 6 cycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted C 2 -C 5 heterocycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted aryl), —C 1 -C 6 alkyl-(substituted or unsubstituted heteroaryl), or —NR D R E ;

R D and R E are independently selected from H, substituted or unsubstituted C 1 -C 6 alkyl, substituted or unsubstituted C 3 -C 6 cycloalkyl, substituted or unsubstituted C 2 -C 5 heterocycloalkyl, substituted or unsubstituted aryl, substituted or unsubstituted heteroaryl, —C 1 -C 6 alkyl-(substituted or unsubstituted C 3 -C 6 cycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted C 2 -C 5 heterocycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted aryl), or —C 1 -C 6 alkyl-(substituted or unsubstituted heteroaryl);

R 3 is C 1 -C 3 alkyl or C 1 -C 3 fluoroalkyl;

each R 5 is independently selected from H, C 1 -C 3 alkyl, C 1 -C 3 haloalkyl, and —C 1 -C 3 alkyl-(C 3 -C 5 cycloalkyl);

each R 7 is independently selected from C 1 -C 6 alkyl, C 1 -C 6 haloalkyl, a substituted or unsubstituted C 3 -C 10 cycloalkyl, a substituted or unsubstituted C 2 -C 10 heterocycloalkyl, a substituted or unsubstituted aryl, a substituted or unsubstituted heteroaryl, —C 1 -C 6 alkyl-(substituted or unsubstituted C 3 -C 10 cycloalkyl), —C 1 -C 6 alkyl-(substituted or unsubstituted C 2 -C 10 heterocycloalkyl, —C 1 -C 6 alkyl-(substituted or unsubstituted aryl), —C 1 -C 6 alkyl-(substituted or unsubstituted heteroaryl), —(CH 2 ) P —CH(substituted or unsubstituted aryl) 2 , —(CH 2 ) P —CH(substituted or unsubstituted heteroaryl) 2 , —(CH 2 ) P —CH(substituted or unsubstituted aryl)(substituted or unsubstituted heteroaryl), -(substituted or unsubstituted aryl)-(substituted or unsubstituted aryl), -(substituted or unsubstituted aryl)-(substituted or unsubstituted heteroaryl), -(substituted or unsubstituted heteroaryl)-(substituted or unsubstituted aryl), and -(substituted or unsubstituted heteroaryl)-(substituted or unsubstituted heteroaryl);

p is 0, 1, or 2;

R 8a and R 8b are independently selected from H, C 1 -C 6 alkyl, and C 1 -C 6 fluoroalkyl;

R 8C and R 8d are independently selected from H, C 1 -C 6 alkyl, and C 1 -C 6 fluoroalkyl;

where each substituted alkyl, cycloalkyl, heterocycloalkyl, aryl, or heteroaryl is substituted with 1-3 R 9 ; and

each R 9 is independently selected from halogen, —OH, —SH, (C═O), CN, C 1 -C 4 alkyl, C 1 -C 4 fluoroalkyl, C 1 -C 4 alkoxy, C 1 -C 4 fluoroalkoxy, —NH 2 , —NH(C 1 -C 4 alkyl), —NH(C 1 -C 4 alkyl) 2 , —C(═O)OH, —C(═O)NH 2 , —C(═O)C 1 -C 3 alkyl, —S(═O) 2 CH 3 , —NH(C 1 -C 4 alkyl)-OH, —NH(C 1 -C 4 alkyl)-O—(C 1 -C 4 alkyl), —O(C 1 -C 4 alkyl)-NH 2 , —O(C 1 -C 4 alkyl)-NH—(C 1 -C 4 alkyl), and —O(C 1 -C 4 alkyl)-N—(C 1 -C 4 alkyl) 2 ; or two R 9 together with the atoms to which they are attached form a methylene dioxy or ethylene dioxy ring substituted or unsubstituted with halogen, —OH, or C 1 -C 3 alkyl;

where each heterocycloalkyl is independently selected from a monocyclic, fused bicyclic, and bridged bicyclic ring, where the heterocycloalkyl has from 2 to 10 carbons in the ring and heteroatoms selected from O, N, or S; and

where each heteroaryl is independently selected from a monocyclic and fused bicyclic ring, where the heteroaryl is a 5- to 14-membered ring system comprising one to thirteen carbon atoms, one to six heteroatoms selected from the group consisting of O, N, or S.

13. The compound of claim 12 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, wherein:

W 2 is C(R 8c )(R 8d );

R 1 is H;

R 2a and R 2b are independently selected from H and C 1 -C 3 alkyl;

and

R 8a , R 8b , R 8c , R 8d are independently selected from H and C 1 -C 3 alkyl.

14. The compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, wherein,

R 7 is selected from

15. The compound of claim 1 or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, selected from:

16. A pharmaceutical composition comprising a compound of claim 1 , or pharmaceutically acceptable salt, N-oxide, racemate, or stereoisomer thereof, and a pharmaceutically acceptable carrier.

Assignments (2)
CHANGE OF NAME Recorded Feb 10, 2020
From: SANFORD-BURNHAM MEDICAL RESEARCH INSTITUTE
To: SANFORD BURNHAM PREBYS MEDICAL DISCOVERY INSTITUTE
Reel/Frame 052181/0736 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Jan 10, 2020
From: COSFORD, NICHOLAS DAVID PETER; VAMOS, MITCHELL DENNIS
To: SANFORD-BURNHAM MEDICAL RESEARCH INSTITUTE
Reel/Frame 051484/0010 →
Continuity (5)
Continuation 16031837 · Jul 10, 2018
Continuation 15363935 · Nov 29, 2016
Continuation 14648435
Provisional Application 61731794 · Nov 30, 2012
Related Publication 20200317731A1 · Oct 8, 2020
Cited By (2)
US 12,678,509 US 12,729,208