IP Library Granted Patent US 11,229,647
Granted Patent B2
US 11,229,647 · App. 16/994,368 · Granted Jan 25, 2022

Methods for treating cholestasis

Inventors: Thomas Jaecklin (Delemont, CH); Alejandro Dorenbaum (Mill Valley, CA)
Assignee: MIRUM PHARMACEUTICALS, INC.
A61K31/4995A61K31/554A61K31/7042A61P1/16A61P17/04
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Quick Facts
Patent No.
US 11,229,647
App. No.
16/994,368
Granted
Jan 25, 2022
Kind
B2
Abstract

Provided herein are methods for treating cholestasis in a subject having a liver disease. The method includes administering to the subject an Apical Sodium-dependent Bile Acid Transporter (ASBTI). More specifically, the present invention relates to methods for treating cholestasis in a subject where the method includes administering an ASBTI to a subject at a dose of at least 10 μg/kg/day.

Claims (16)

1. A method for treating Alagille Syndrome (ALGS) in a pediatric subject in need of such treatment comprising administering to the subject

(maralixibat chloride), wherein maralixibat chloride is administered in an amount of from about 400 μg/kg/day to about 800 μg/kg/day.

2. The method of claim 1 , wherein maralixibat chloride is administered once daily (QD).

3. The method of claim 1 , wherein maralixibat chloride is administered twice daily (BID).

4. The method of claim 1 , wherein maralixibat chloride is administered for at least 18 weeks.

5. The method of claim 1 , wherein maralixibat chloride is administered for at least 2 years.

6. The method of claim 1 , wherein maralixibat chloride is administered for at least 3 years.

7. The method of claim 1 , wherein the subject exhibits below normal height or weight prior to the administration of maralixibat chloride.

8. The method of claim 1 , wherein the subject experiences pruritus prior to the administration of maralixibat chloride.

9. The method of claim 1 , wherein the subject is at least 1 year of age.

10. The method of claim 1 , wherein maralixibat chloride is administered prior to ingestion of food.

11. The method of claim 1 , wherein maralixibat chloride is administered orally.

12. A method for treating Alagille Syndrome (ALGS) in a pediatric subject in need of such treatment comprising administering to the subject

(maralixibat chloride), wherein maralixibat chloride is administered in an amount of about 400 μg/kg/day.

13. A method for treating Alagille Syndrome (ALGS) in a pediatric subject in need of such treatment comprising administering to the subject

(maralixibat chloride), wherein maralixibat chloride is administered in an amount of about 800 μg/kg/day.

Assignments (8)
CHANGE OF ADDRESS Recorded Aug 15, 2024
From: MIRUM PHARMACEUTICALS, INC.
To: MIRUM PHARMACEUTICALS, INC.
Reel/Frame 068654/0513 →
CHANGE OF ADDRESS Recorded Jun 10, 2024
From: MIRUM PHARMACEUTICALS, INC.
To: MIRUM PHARMACEUTICALS, INC.
Reel/Frame 067680/0956 →
RELEASE OF SECURITY INTEREST Recorded Apr 20, 2023
From: MULHOLLAND SA LLC
To: MIRUM PHARMACEUTICALS, INC.
Reel/Frame 063383/0795 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Dec 6, 2021
From: SHIRE HUMAN GENETIC THERAPIES, INC.
To: MIRUM PHARMACEUTICALS, INC.
Reel/Frame 058320/0798 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Dec 6, 2021
From: DORENBAUM, ALEJANDRO
To: SHIRE HUMAN GENETIC THERAPIES, INC.
Reel/Frame 058311/0209 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Nov 9, 2021
From: DORENBAUM, ALEJANDRO
To: MIRUM PHARMACEUTICALS, INC.
Reel/Frame 058063/0200 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Sep 22, 2021
From: JAECKLIN, THOMAS
To: MIRUM PHARMACEUTICALS, INC.
Reel/Frame 057565/0748 →
SECURITY INTEREST Recorded Dec 9, 2020
From: MIRUM PHARMACEUTICALS, INC.
To: MULHOLLAND SA LLC
Reel/Frame 054598/0910 →
Continuity (6)
Continuation PCTUS2020017941 · Feb 12, 2020
Provisional Application 62804523 · Feb 12, 2019
Provisional Application 62863904 · Jun 20, 2019
Provisional Application 62908431 · Sep 30, 2019
Provisional Application 62932015 · Nov 7, 2019
Related Publication 20200375989A1 · Dec 3, 2020
Cited By (2)
US 12,576,079 US 12,599,602