IP Library Granted Patent US 11,834,470
Granted Patent B2
US 11,834,470 · App. 17/281,424 · Granted Dec 5, 2023

4-thioribose NAD analogues and methods of synthesizing and using the same

Inventors: Yong Zhang (Los Angeles, CA); Zhefu Dai (Los Angeles, CA); Xiao-Nan Zhang (Los Angeles, CA)
Assignee: UNIVERSITY OF SOUTHERN CALIFORNIA
C07H19/20A61K31/7076C12P19/28
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Quick Facts
Patent No.
US 11,834,470
App. No.
17/281,424
Granted
Dec 5, 2023
Kind
B2
Abstract

This disclosure provides a method of synthesis of 4′-thioribose NAD+ and analogues thereof, using an efficient chemoenzymatic approach. Also provided are methods of inhibiting the CD38 enzyme and compounds including 4′-thioribose NAD+ and compounds related thereto.

Claims (25)

1. A method of synthesizing a compound of formula I:

or a pharmaceutically acceptable salt or solvate thereof, comprising the step of enzymatically converting a compound of formula IV:

to the compound of formula I.

2. The method of claim 1 , wherein enzymatically converting the compound of formula IV to the compound of formula I comprises contacting the compound of formula IV with adenosine triphosphate (ATP), nicotinamide riboside kinase (NRK), and nicotinamide mononucleotide adenylyltransferase (NMNAT).

3. The method of claim 1 , wherein the contacting is for less than 5 hours.

4. The method of claim 1 , further comprising the step of converting a compound of formula II:

into a compound of formula III:

wherein R 4 is an optionally substituted C 1 -C 8 alkyl;

P 1 , P 2 and P 3 are protecting groups each independently selected from the group consisting of 2,2,2-trichloroethyl carbonate (Troc), 2-methoxyethoxymethyl ether (MEM), 2-naphthylmethyl ether (Nap), 4-methoxybenzyl ether (PMB), acetate (Ac), benzoate (Bz), benzyl ether (Bn), benzyloxymethyl acetal (BOM), benzyloxymethyl acetal (BOM), methoxymethyl acetal (MOM), methoxypropyl acetal (MOP), methyl ether, tetrahydropyranyl acetal (THP), triethylsilyl ether (TES), triisopropylsilyl ether (TIPS), trimethylsilyl ether (TMS), tert-Butyldimethylsilyl ether (TBS, TBDMS), and tert-butyldiphenylsilyl ether (TBDPS); or P 2 and P 3 together with the oxygens to which they are attached, together form an acetonide, benzaldehyde acetal or carbonate.

5. The method of claim 4 , wherein R 4 is methyl.

6. The method of claim 4 , wherein P 1 is Bz.

7. The method of claim 4 , wherein P 2 and P 3 along with the oxygens to which they are attached, together form an acetonide.

8. The method of claim 4 , further comprising the step of deprotecting the compound of formula III to produce the compound of formula IV.

9. The method of claim 8 , wherein:

P 1 is Bz;

P 2 and P 3 along with the oxygens to which they are attached, together form an acetonide; and

wherein deprotecting the compound of formula III to produce the compound of formula IV comprises contacting the compound of formula III with trifluoroacetic acid (TFA) to produce a compound of formula V:

followed by deprotection of the compound of formula V to produce the compound of formula IV.

10. The method of claim 9 , wherein deprotection of the compound of formula V to produce the compound of formula IV comprises contacting the compound of formula V with ammonia and methanol.

11. A method of inhibiting enzymatic activity of CD38, comprising contacting CD38 with a compound of formula I or pharmaceutically acceptable salts and solvates thereof:

12. A compound of formula I-A and pharmaceutically acceptable salts and solvates thereof:

wherein R 3 is selected from thymine, cytosine, adenine, uracil or guanine.

13. The compound of claim 12 , of formula I:

14. A pharmaceutical composition comprising a pharmaceutically effective amount the compound of claim 12 and a carrier.

15. A kit comprising the compound of claim 12 and instructions for use.

Assignments (2)
CONFIRMATORY LICENSE Recorded Nov 22, 2023
From: UNIVERSITY OF SOUTHERN CALIFORNIA
To: NATIONAL INSTITUTES OF HEALTH (NIH), U.S. DEPT. OF HEALTH AND HUMAN SERVICES (DHHS), U.S. GOVERNMENT
Reel/Frame 065666/0460 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Mar 30, 2021
From: ZHANG, YONG; DAI, ZHEFU; ZHANG, XIAO-NAN
To: UNIVERSITY OF SOUTHERN CALIFORNIA
Reel/Frame 055769/0792 →
Continuity (2)
Provisional Application 62742212 · Oct 5, 2018
Related Publication 20220227803A1 · Jul 21, 2022