IP Library › Granted Patent US 11,447,527
Granted Patent B2
US 11,447,527 · App. 17/382,092 · Granted Sep 20, 2022

Endogenous Gag-based capsids and uses thereof

Inventors: Colin Malone (Brooklyn, NY); Ian Peikon (Bethpage, NY); Zachary Gilbert (Brooklyn, NY); Andrey Pisarev (Long Beach Township, NJ); Adam Fraites (Long Beach Township, NJ); Jessica Crisp (Phoenix, AZ)
Assignee: VNV NEWCO INC.
C07K14/005A61K38/00A61K48/0008C07K14/435C07K14/46C07K16/00C12N9/22C12N15/11C12N15/87C12N15/907C12N2310/20
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Quick Facts
Patent No.
US 11,447,527
App. No.
17/382,092
Granted
Sep 20, 2022
Kind
B2
Abstract

Disclosed herein, in certain embodiments, are recombinant Arc and endogenous Gag polypeptides, and methods of using recombinant Arc and endogenous Gag polypeptides.

Claims (36)

1. A capsid comprising a recombinant endogenous Gag polypeptide and a heterologous cargo that is not native to the endogenous Gag polypeptide, wherein the endogenous Gag polypeptide is not an Arc polypeptide.

2. The capsid of claim 1 , wherein the endogenous Gag polypeptide is a Paraneoplastic Ma antigen family polypeptide.

3. The capsid of claim 2 , wherein the Paraneoplastic Ma antigen family polypeptide comprises:

a) an amino acid sequence that is SEQ ID NO: 16 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 16;

b) an amino acid sequence that is SEQ ID NO: 17 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 17;

c) an amino acid sequence that is SEQ ID NO: 18 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 18;

d) an amino acid sequence that is SEQ ID NO: 19 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 19; or

e) an amino acid sequence that is SEQ ID NO: 27 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 27.

4. The capsid of claim 2 , wherein the heterologous cargo is a nucleic acid.

5. The capsid of claim 4 , wherein the heterologous cargo is an RNA.

6. The capsid of claim 2 , wherein the heterologous cargo is a therapeutic agent.

7. The capsid of claim 2 , wherein the heterologous cargo is a polypeptide.

8. The capsid of claim 2 , wherein the heterologous cargo is a gene editing system.

9. The capsid of claim 2 , further comprising a second polypeptide.

10. The capsid of claim 9 , wherein the second polypeptide is an antibody or binding fragment thereof.

11. The capsid of claim 9 , wherein the second polypeptide binds to a target site.

12. The capsid of claim 2 , further comprising a delivery component that comprises a microvesicle, a microparticle, a liposome, or a micelle.

13. The capsid of claim 2 , further comprising a delivery component that comprises an extracellular vesicle.

14. The capsid of claim 1 , wherein the endogenous Gag polypeptide is a retrotransposon Gag-like family polypeptide.

15. The capsid of claim 14 , wherein the retrotransposon Gag-like family polypeptide comprises:

a) an amino acid sequence that is SEQ ID NO: 20 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 20;

b) an amino acid sequence that is SEQ ID NO: 21 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 21;

c) an amino acid sequence that is SEQ ID NO: 22 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 22;

d) an amino acid sequence that is SEQ ID NO: 23 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 23;

e) an amino acid sequence that is SEQ ID NO: 24 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 24; or

f) an amino acid sequence that is SEQ ID NO: 28 or an amino acid sequence that is at least 90% identical to the SEQ ID NO: 28.

16. The capsid of claim 14 , wherein the heterologous cargo is a nucleic acid.

17. The capsid of claim 16 , wherein the heterologous cargo is an RNA.

18. The capsid of claim 14 , wherein the heterologous cargo is a therapeutic agent.

19. The capsid of claim 14 , wherein the heterologous cargo is a polypeptide.

20. The capsid of claim 14 , wherein the heterologous cargo is a gene editing system.

21. The capsid of claim 14 , further comprising a second polypeptide.

22. The capsid of claim 21 , wherein the second polypeptide is an antibody or binding fragment thereof.

23. The capsid of claim 21 , wherein the second polypeptide binds to a target site.

24. The capsid of claim 14 , further comprising a delivery component that comprises a microvesicle, a microparticle, a liposome, or a micelle.

25. The capsid of claim 14 , further comprising a delivery component that comprises an extracellular vesicle.

Assignments (3)
CHANGE OF NAME Recorded Jul 22, 2023
From: VNV NEWCO INC.
To: AERA THERAPEUTICS, INC.
Reel/Frame 064347/0692 →
CORRECTIVE ASSIGNMENT TO CORRECT THE THIRD INVENTOR'S FIRST NAME PREVIOUSLY RECORDED AT REEL: 057466 FRAME: 0976. ASSIGNOR(S) HEREBY CONFIRMS THE ASSIGNMENT . Recorded Oct 7, 2021
From: MALONE, COLIN; PEIKON, IAN; GILBERT, ZACHARY; PISAREV, ANDREY; FRAITES, ADAM; CRISP, JESSICA
To: VNV NEWCO INC.
Reel/Frame 057748/0412 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Sep 13, 2021
From: MALONE, COLIN; PEIKON, IAN; GILBERT, ZACH; PISAREV, ANDREY; FRAITES, ADAM; CRISP, JESSICA
To: VNV NEWCO INC.
Reel/Frame 057466/0976 →
Continuity (3)
Continuation 17277119
Provisional Application 62733015 · Sep 18, 2018
Related Publication 20210347829A1 · Nov 11, 2021
Cited By (5)
US 12,319,938 US 12,351,814 US 12,351,815 US 12,404,525 US 12,617,822