IP Library Granted Patent US 12,404,300
Granted Patent B2
US 12,404,300 · App. 17/414,103 · Granted Sep 2, 2025

Mitochondria-targeting peptides

Inventors: Guozhu Zheng (Lexington, MA); Mark J. Bamberger (South Glastonbury, CT); Inese Smukste (Weston, MA)
Assignee: Stealth BioTherapeutics Inc.
C07K5/1016A61P9/10C07K7/06A61K38/00
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Quick Facts
Patent No.
US 12,404,300
App. No.
17/414,103
Granted
Sep 2, 2025
Kind
B2
Abstract

Disclosed are analogs of SBT-20. The compounds are useful for the treatment and prevention of ischemia-reperfusion injury (e.g., cardiac ischemia-reperfusion injury) or myocardial infarction.

Claims (30)

1. A compound of formula (I), or a pharmaceutically acceptable salt thereof:

wherein:

Aaa 1 is an amino acid residue selected from the group consisting of:

Aaa 2 is an amino acid residue selected from the group consisting of:

Aaa 3 is an amino acid residue selected from the group consisting of:

Aaa 4 is an amino acid residue selected from the group consisting of:

R 1a and R 4d are each independently (C 1 -C 6 )alkyl;

R 2a , R 2b , R 2e , R 3a , R 3b , R 4a , R 4b , R 4c are each independently selected from the group consisting of H and (C 1 -C 6 )alkyl; and

R a , R b , R 2c , and R 2d are each independently selected from the group consisting of H, (C 1 -C 6 )alkyl, C(O)((C 1 -C 6 )alkyl), C(O)((C 1 -C 6 ) haloalkyl), C(O)O((C 1 -C 6 )alkyl), and C(O)O(aryl (C 1 -C 6 )alkyl).

2. The compound of claim 1 , wherein Aaa 1 is selected from the group consisting of:

3. The compound of claim 2 , wherein Aaa 1 is

4. The compound of claim 1 , wherein Aaa 1 is an amino acid residue selected from the group consisting of:

5. The compound of claim 1 , wherein Aaa 2 is selected from the group consisting of:

6. The compound of claim 1 , wherein Aaa 2 is

7. The compound of claim 1 , wherein Aaa 3 is selected from the group consisting of:

8. The compound of claim 1 , wherein Aaa 3 is selected from the group consisting of:

9. The compound of claim 1 , wherein Aaa 3 is selected from the group consisting of:

10. The compound of claim 1 , wherein Aaa 4 is selected from the group consisting of:

11. The compound of claim 1 , wherein Aaa 4 is selected from the group consisting of:

12. The compound of claim 1 , wherein Aaa 4 is selected from the group consisting of:

13. The compound of claim 1 , wherein R a and R b are each independently H or methyl.

14. The compound of claim 1 , wherein R a and R b are each H.

15. The compound of claim 1 , or a pharmaceutically acceptable salt thereof, selected from the following table:

16. A pharmaceutical composition, comprising a compound of claim 1 , or a pharmaceutically acceptable salt thereof; and a pharmaceutically acceptable carrier.

17. The compound of claim 15 , or a pharmaceutically acceptable salt thereof, wherein the compound is:

18. The compound of claim 15 , or a pharmaceutically acceptable salt thereof, wherein the compound is:

19. A method for treating or preventing ischemia-reperfusion injury in a subject in need thereof comprising administering to the subject a therapeutically effective amount of a compound of claim 1 , or a pharmaceutically acceptable salt thereof.

20. The method of claim 19 , wherein the ischemia-reperfusion injury is cardiac ischemia-reperfusion injury.

21. A method for treating or preventing a myocardial infarction in a subject in need thereof comprising administering to the subject a therapeutically effective amount of a compound of claim 1 , or a pharmaceutically acceptable salt thereof.

22. The method of claim 19 , wherein the compound is administered orally, topically, systemically, intravenously, subcutaneously, intraperitoneally, or intramuscularly.

Assignments (2)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Apr 27, 2022
From: ZHENG, GUOZHU; BAMBERGER, MARK J.; SMUKSTE, INESE
To: STEALTH BIOTHERAPEUTICS CORP.
Reel/Frame 059751/0381 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Apr 27, 2022
From: STEALTH BIOTHERAPEUTICS CORP.
To: STEALTH BIOTHERAPEUTICS INC.
Reel/Frame 059806/0537 →
Continuity (3)
Provisional Application 62892939 · Aug 28, 2019
Provisional Application 62781153 · Dec 18, 2018
Related Publication 20220041653A1 · Feb 10, 2022
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