IP Library › Granted Patent US 11,357,867
Granted Patent B2
US 11,357,867 · App. 17/495,949 · Granted Jun 14, 2022

Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses therefor

Inventors: James M. Wilson (Philadelphia, PA); Guangping Gao (Westborough, MA); Mauricio R. Alvira (Philadelphia, PA); Luc H. Vandenberghe (Weston, MA)
Assignee: The Trustees of the University of Pennsylvania
A61K48/00C07K14/005C07K14/705C12N7/00C12N9/644C12N15/86C12Y304/21022C12N2750/14121C12N2750/14122C12N2750/14142C12N2750/14143C12N2750/14151C12N2830/008C12N2830/48C12N2830/85
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Quick Facts
Patent No.
US 11,357,867
App. No.
17/495,949
Granted
Jun 14, 2022
Kind
B2
Abstract

Sequences of novel adeno-associated virus capsids and vectors and host cells containing these sequences are provided. Also described are methods of using such host cells and vectors in production of rAAV particles. AAV-mediated delivery of therapeutic and immunogenic genes using the vectors of the invention is also provided.

Claims (12)

1. A cultured host cell containing a recombinant nucleic acid molecule encoding an AAV vp1 capsid protein having a sequence comprising amino acids 1 to 736 of SEQ ID NO: 123 (AAV9), wherein the recombinant nucleic acid molecule further comprises a heterologous non-AAV sequence, and wherein the recombinant nucleic acid molecule is a plasmid.

2. The cultured host cell according to claim 1 , which further comprises a functional rep gene.

3. The cultured host cell according to claim 2 , wherein the rep gene is from AAV2.

4. A cultured host cell containing a recombinant nucleic acid molecule encoding an AAV vp2 capsid protein having a sequence comprising amino acids 138 to 736 of SEQ ID NO: 123 (AAV9), wherein the recombinant nucleic acid molecule further comprises a heterologous non-AAV sequence, and wherein the recombinant nucleic acid molecule is a plasmid.

5. The cultured host cell according to claim 4 , which further comprises a functional rep gene.

6. The cultured host cell according to claim 5 , wherein the rep gene is from AAV2.

7. A cultured host cell containing a recombinant nucleic acid molecule encoding an AAV vp3 capsid protein having a sequence comprising amino acids 203 to 736 of SEQ ID NO: 123 (AAV9), wherein the recombinant nucleic acid molecule further comprises a heterologous non-AAV sequence, and wherein the recombinant nucleic acid molecule is a plasmid.

8. The cultured host cell according to claim 7 , which further comprises a functional rep gene.

9. The cultured host cell according to claim 8 , wherein the rep gene is from AAV2.

10. A cultured host cell containing a recombinant nucleic acid molecule comprising (a) nucleotides 1 to 2208 of SEQ ID NO: 3, (b) nucleotides 412 to 2208 of SEQ ID NO: 3, or (c) nucleotides 607 to 2208 of SEQ ID NO: 3, wherein the recombinant nucleic acid molecule further comprises a heterologous non-AAV sequence, and wherein the recombinant nucleic acid molecule is a plasmid.

11. The cultured host cell according to claim 10 , which further comprises a rep gene.

12. The cultured host cell according to claim 11 , wherein the rep gene is from AAV2.

Assignments (1)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded May 2, 2022
From: WILSON, JAMES M.; GAO, GUANGPING; ALVIRA, MAURICIO R.; VANDENBERGHE, LUK
To: THE TRUSTEES OF THE UNIVERSITY OF PENNSYLVANIA
Reel/Frame 059781/0532 →
Continuity (9)
Continuation 17151527 · Jan 18, 2021
Continuation 16776850 · Jan 30, 2020
Continuation 16045043 · Jul 25, 2018
Continuation 15227418 · Aug 3, 2016
Continuation 13023918 · Feb 9, 2011
Continuation 10573600
Provisional Application 60566546 · Apr 29, 2004
Provisional Application 60508226 · Sep 30, 2003
Related Publication 20220025400A1 · Jan 27, 2022
Cited By (2)
US 12,600,989 US 12,612,647