Antigen-binding protein constructs and uses thereof
Provided herein are antigen-binding protein constructs and uses of the same.
1 . A pharmaceutical composition comprising an effective amount of an antigen-binding protein construct (ABPC) comprising:
a first antigen-binding domain that is capable of specifically binding CD123 or an epitope of CD123 presented on the surface of a target mammalian cell,
wherein the first antigen-binding domain comprises:
a heavy chain variable domain of SEQ ID NO: 1 and a light chain variable domain of SEQ ID NO: 64, SEQ ID NO: 70, SEQ ID NO: 74, SEQ ID NO: 77, SEQ ID NO: 78, or SEQ ID NO: 79; or
a heavy chain variable domain of SEQ ID NO: 14, SEQ ID NO: 15, SEQ ID NO: 16, SEQ ID NO: 17, SEQ ID NO: 20, SEQ ID NO: 22, SEQ ID NO: 26, SEQ ID NO: 40, SEQ ID NO: 46, SEQ ID NO: 47, SEQ ID NO: 48, SEQ ID NO: 49, SEQ ID NO: 50, SEQ ID NO: 51, SEQ ID NO: 52, SEQ ID NO: 81, SEQ ID NO: 82, SEQ ID NO: 83, SEQ ID NO: 84, SEQ ID NO: 85, SEQ ID NO: 86, SEQ ID NO: 87, SEQ ID NO: 88, SEQ ID NO: 89, SEQ ID NO: 90, SEQ ID NO: 91, SEQ ID NO: 92, SEQ ID NO: 93, SEQ ID NO: 94, SEQ ID NO: 95, SEQ ID NO: 96, SEQ ID NO: 97, SEQ ID NO: 98, SEQ ID NO: 99, or SEQ ID NO: 100 and a light chain variable domain of SEQ ID NO: 2;
and wherein:
(i) the dissociation rate of the first antigen-binding domain at a pH of about 4.0 to about 6.5 is faster than the dissociation rate at a pH of about 7.0 to about 8.0; or
(ii) the dissociation constant (K D ) of the first antigen-binding domain at a pH of about 4.0 to about 6.5 is greater than the Kp at a pH of about 7.0 to about 8.0.
2 . The pharmaceutical composition of claim 1 , wherein the ABPC is degraded in the target mammalian cell following internalization of the ABPC by the target mammalian cell.
3 . The pharmaceutical composition of claim 1 , wherein the ABPC further comprises a conjugated toxin, radioisotope, drug, or small molecule.
4 . A pharmaceutical composition comprising an effective amount of an antigen-binding protein construct (ABPC) comprising:
a first antigen-binding domain that is capable of specifically binding CD123 or an epitope of CD123 presented on the surface of a target mammalian cell; and
a conjugated toxin, radioisotope, drug, or small molecule,
wherein the first antigen-binding domain comprises:
a heavy chain variable domain of SEQ ID NO: 1 and a light chain variable domain of SEQ ID NO: 64, SEQ ID NO: 70, SEQ ID NO: 74, SEQ ID NO: 77, SEQ ID NO: 78, or SEQ ID NO: 79; or
a heavy chain variable domain of SEQ ID NO: 14, SEQ ID NO: 15, SEQ ID NO: 16, SEQ ID NO: 17, SEQ ID NO: 20, SEQ ID NO: 22, SEQ ID NO: 26, SEQ ID NO: 40, SEQ ID NO: 46, SEQ ID NO: 47, SEQ ID NO: 48, SEQ ID NO: 49, SEQ ID NO: 50, SEQ ID NO: 51, SEQ ID NO: 52, SEQ ID NO: 81, SEQ ID NO: 82, SEQ ID NO: 83, SEQ ID NO: 84, SEQ ID NO: 85, SEQ ID NO: 86, SEQ ID NO: 87, SEQ ID NO: 88, SEQ ID NO: 89, SEQ ID NO: 90, SEQ ID NO: 91, SEQ ID NO: 92, SEQ ID NO: 93, SEQ ID NO: 94, SEQ ID NO: 95, SEQ ID NO: 96, SEQ ID NO: 97, SEQ ID NO: 98, SEQ ID NO: 99, or SEQ ID NO: 100 and a light chain variable domain of SEQ ID NO: 2;
and wherein:
(i) the dissociation rate of the first antigen-binding domain at a pH of about 4.0 to about 6.5 is faster than the dissociation rate at a pH of about 7.0 to about 8.0; or
the dissociation constant (K D ) of the first antigen-binding domain at a pH of about 4.0 to about 6.5 is greater than the K D at a pH of about 7.0 to about 8.0; and
(ii) the composition provides for one or more of:
an increase in toxin liberation in the target mammalian cell as compared to a composition comprising the same amount of a control ABPC comprising a heavy chain variable domain of SEQ ID NO: 1 and a light chain variable domain of SEQ ID NO: 2;
an increase in target mammalian cell killing as compared to a composition comprising the same amount of the control ABPC; and
an increase in endolysosomal delivery in the target mammalian cell as compared to a composition comprising the same amount of the control ABPC.
5 . The pharmaceutical composition of claim 4 , wherein the composition provides for:
an increase in toxin liberation in the target mammalian cell as compared to a composition comprising the same amount of the control ABPC; and/or
an increase in target mammalian cell killing as compared to a composition comprising the same amount of the control ABPC.
6 . The pharmaceutical composition of claim 1 , wherein the composition provides for an increase in endolysosomal delivery in the target mammalian cell as compared to a composition comprising the same amount of a control ABPC.
7 . The pharmaceutical composition of claim 1 , wherein the composition:
results in less of a reduction in the level of CD123 presented on the surface of the target mammalian cell as compared to a composition comprising the same amount of a control ABPC comprising a heavy chain variable domain of SEQ ID NO: 1 and a light chain variable domain of SEQ ID NO: 2; or
does not result in a detectable reduction in the level of CD123 presented on the surface of the target mammalian cell.
8 . The pharmaceutical composition of claim 1 , wherein the target mammalian cell is a cancer cell.
9 . The pharmaceutical composition of claim 1 , wherein the ABPC is cytotoxic or cytostatic to the target mammalian cell.
10 . The pharmaceutical composition of claim 1 , wherein the ABPC comprises a single polypeptide.
11 . The pharmaceutical composition of claim 10 , wherein the antigen-binding domain is an scFv.
12 . The pharmaceutical composition of claim 1 , wherein the ABPC comprises two or more polypeptides.
13 . The pharmaceutical composition of claim 12 , wherein the ABPC is an antibody.
14 . The pharmaceutical composition of claim 1 , wherein the ABPC further comprises a second antigen-binding domain.
15 . An antigen-binding protein construct (ABPC) comprising:
a first antigen-binding domain that is capable of specifically binding CD123 or an epitope of CD123 presented on the surface of a target mammalian cell,
wherein the first antigen-binding domain comprises:
a heavy chain variable domain of SEQ ID NO: 1 and a light chain variable domain of SEQ ID NO: 64, SEQ ID NO: 70, SEQ ID NO: 74, SEQ ID NO: 77, SEQ ID NO: 78, or SEQ ID NO: 79; or
a heavy chain variable domain of SEQ ID NO: 14, SEQ ID NO: 15, SEQ ID NO: 16, SEQ ID NO: 17, SEQ ID NO: 20, SEQ ID NO: 22, SEQ ID NO: 26, SEQ ID NO: 40, SEQ ID NO: 46, SEQ ID NO: 47, SEQ ID NO: 48, SEQ ID NO: 49, SEQ ID NO: 50, SEQ ID NO: 51, SEQ ID NO: 52, SEQ ID NO: 81, SEQ ID NO: 82, SEQ ID NO: 83, SEQ ID NO: 84, SEQ ID NO: 85, SEQ ID NO: 86, SEQ ID NO: 87, SEQ ID NO: 88, SEQ ID NO: 89, SEQ ID NO: 90, SEQ ID NO: 91, SEQ ID NO: 92, SEQ ID NO: 93, SEQ ID NO: 94, SEQ ID NO: 95, SEQ ID NO: 96, SEQ ID NO: 97, SEQ ID NO: 98, SEQ ID NO: 99, or SEQ ID NO: 100 and a light chain variable domain of SEQ ID NO: 2;
and wherein:
(i) the dissociation rate of the first antigen-binding domain at a pH of about 4.0 to about 6.5 is faster than the dissociation rate at a pH of about 7.0 to about 8.0; or
(ii) the dissociation constant (K D ) of the first antigen-binding domain at a pH of about 4.0 to about 6.5 is greater than the Kp at a pH of about 7.0 to about 8.0.
16 . An antigen-binding protein construct (ABPC) comprising:
a first antigen-binding domain that is capable of specifically binding CD123 or an epitope of CD123 presented on the surface of a target mammalian cell; and
a conjugated toxin, radioisotope, drug, or small molecule,
wherein the first antigen-binding domain comprises:
a heavy chain variable domain of SEQ ID NO: 1 and a light chain variable domain of SEQ ID NO: 64, SEQ ID NO: 70, SEQ ID NO: 74, SEQ ID NO: 77, SEQ ID NO: 78, or SEQ ID NO: 79; or
a heavy chain variable domain of SEQ ID NO: 14, SEQ ID NO: 15, SEQ ID NO: 16, SEQ ID NO: 17, SEQ ID NO: 20, SEQ ID NO: 22, SEQ ID NO: 26, SEQ ID NO: 40, SEQ ID NO: 46, SEQ ID NO: 47, SEQ ID NO: 48, SEQ ID NO: 49, SEQ ID NO: 50, SEQ ID NO: 51, SEQ ID NO: 52, SEQ ID NO: 81, SEQ ID NO: 82, SEQ ID NO: 83, SEQ ID NO: 84, SEQ ID NO: 85, SEQ ID NO: 86, SEQ ID NO: 87, SEQ ID NO: 88, SEQ ID NO: 89, SEQ ID NO: 90, SEQ ID NO: 91, SEQ ID NO: 92, SEQ ID NO: 93, SEQ ID NO: 94, SEQ ID NO: 95, SEQ ID NO: 96, SEQ ID NO: 97, SEQ ID NO: 98, SEQ ID NO: 99, or SEQ ID NO: 100 and a light chain variable domain of SEQ ID NO: 2;
and wherein:
(i) the dissociation rate of the first antigen-binding domain at a pH of about 4.0 to about 6.5 is faster than the dissociation rate at a pH of about 7.0 to about 8.0; or
the dissociation constant (K D ) of the first antigen-binding domain at a pH of about 4.0 to about 6.5 is greater than the K D at a pH of about 7.0 to about 8.0; and
(ii) the composition provides for one or more of:
an increase in toxin liberation in the target mammalian cell as compared to a composition comprising the same amount of a control ABPC comprising a heavy chain variable domain of SEQ ID NO: 1 and a light chain variable domain of SEQ ID NO: 2;
an increase in target mammalian cell killing as compared to a composition comprising the same amount of the control ABPC; and
an increase in endolysosomal delivery in the target mammalian cell as compared to a composition comprising the same amount of the control ABPC.
17 . A kit comprising at least one dose of the pharmaceutical composition of claim 1 .
18 . A method of treating a cancer characterized by having a population of cancer cells that have CD123 or an epitope of CD123 presented on their surface, the method comprising:
administering a therapeutically effective amount of the pharmaceutical composition of claim 1 to a subject identified as having a cancer characterized by having the population of cancer cells.
19 . A method of reducing the volume of a tumor in a subject, wherein the tumor is characterized by having a population of cancer cells that have CD123 or an epitope of CD123 presented on their surface, the method comprising:
administering a therapeutically effective amount of the pharmaceutical composition of claim 1 to a subject identified as having a cancer characterized by having the population of cancer cells.
20 . A method of inducing cell death in a cancer cell in a subject, wherein the cancer cell has CD123 or an epitope of CD123 presented on its surface, wherein the method comprises:
administering a therapeutically effective amount of the pharmaceutical composition of claim 1 to a subject identified as having a cancer characterized by having a population of the cancer cells.
21 . A method of decreasing the risk of developing a metastasis or decreasing the risk of developing an additional metastasis in a subject having a cancer, wherein the cancer is characterized by having a population of cancer cells that have CD123 or an epitope of CD123 presented on their surface the method comprising:
administering a therapeutically effective amount of the pharmaceutical composition of claim 1 to a subject identified as having a cancer characterized by having the population of cancer cells.