IP Library › Granted Patent US 12,655,443
Granted Patent B2
US 12,655,443 · App. 17/801,038 · Granted Jun 16, 2026

Enhanced expression system and methods of use thereof

Inventors: Ji Chen (Shanghai, CN); Yu Zhang (Shanghai, CN); Jung-hao Wang (Shanghai, CN); Yarong Li (Shanghai, CN); Bin Zhao (Shanghai, CN); Dujuan Lian (Shanghai, CN); Yuchen Zhang (Shanghai, CN); Cui Huang (Shanghai, CN); Zheng Zhang (Shanghai, CN); Jiexing Cai (Shanghai, CN)
Assignee: WuXi Biologics Ireland Limited
C12N15/85C07K14/70532C07K16/241C12N15/62C07K2319/30C12N2800/90
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Quick Facts
Patent No.
US 12,655,443
App. No.
17/801,038
Granted
Jun 16, 2026
Kind
B2
Abstract

This disclosure relates to an efficient protein expression system that utilizes piggyBac transposons and/or regulatory elements.

Claims (30)

1 . A nucleic acid comprising

a 5′-ITR (inverted terminal repeat) sequence;

a 3′-ITR sequence; and

a regulatory element sequence that is at least 90% identical to a sequence selected from the group consisting of SEQ ID NOs: 36, 43, 46, 48, 55, and 58.

2 . The nucleic acid of claim 1 , wherein the 5′ ITR sequence comprises a sequence that is at least 90% identical to SEQ ID NO: 68, and the 3′ ITR sequence comprises a sequence that is at least 90% identical to SEQ ID NO: 60.

3 . The nucleic acid of claim 1 , wherein the 5′ ITR sequence comprises SEQ ID NO: 68 and the 3′ ITR sequence comprises SEQ ID NO: 60.

4 . The nucleic acid of claim 1 , further comprising a 5′-internal domain and a 3′-internal domain, wherein the 5′-internal domain comprise a sequence that is at least 90% identical to SEQ ID NO: 66, wherein the 3′-internal domain comprise a sequence that is at least 90% identical to SEQ ID NO: 67, wherein the 5′-internal domain is immediately adjacent to the 5′-ITR, and the 3′-internal domain is immediately adjacent to the 3′-ITR.

5 . The nucleic acid of claim 1 , wherein the nucleic acid comprises one or more regulatory element sequences selected from the group consisting of SEQ ID NO: 36 and SEQ ID NO: 48.

6 . The nucleic acid of claim 1 , further comprising a promoter and a sequence encoding a polypeptide, wherein the sequence encoding the polypeptide is operably linked to the promoter.

7 . The nucleic acid of claim 6 , wherein the sequence encoding a polypeptide is located between two regulatory element sequences.

8 . The nucleic acid of claim 1 , further comprising a promoter and a sequence encoding two or more polypeptides, wherein the sequence encoding the two or more polypeptides is operably linked to the promoter.

9 . The nucleic acid of claim 8 , wherein the sequence encoding two or more polypeptides encodes an antibody heavy chain and an antibody light chain.

10 . The nucleic acid of claim 1 , wherein in addition to the regulatory element sequence, the nucleic acid further comprises an additional sequence that is at least 90% identical to a sequence selected from the group consisting of SEQ ID NOs: 36 and 48.

11 . The nucleic acid of claim 1 , wherein the nucleic acid comprises two or more expression cassettes.

12 . The nucleic acid of claim 1 , wherein the nucleic acid comprises a selection marker.

13 . The nucleic acid of claim 12 , wherein the selection marker is an antibiotic resistance gene, a sequence encoding a fluorescent protein, or lacZ.

14 . The nucleic acid of claim 1 , wherein the 5′-ITR comprises a TR L , a 5′-ITR spacer and an IR L , and the 3′-ITR comprises an IR R , a 3′-ITR spacer and a TR R .

15 . The nucleic acid of claim 14 , wherein the TR L comprises a sequence that is at least 90% identical to a reverse sequence or a reverse complementary sequence of SEQ ID NO: 61; wherein the 5′-ITR spacer comprises a sequence that is at least 90% identical to a reverse sequence or a reverse complementary sequence of SEQ ID NO: 62; wherein the IR L comprises a sequence that is at least 90% identical to a reverse sequence or a reverse complementary sequence of SEQ ID NO: 63; wherein the TR R comprises a sequence that is at least 90% identical to a reverse sequence or a reverse complementary sequence of SEQ ID NO: 64; and wherein the IR R comprises a sequence that is at least 90% identical to a reverse sequence or a reverse complementary sequence of SEQ ID NO: 65.

16 . The nucleic acid of claim 1 , wherein the regulatory element sequence is at least 90% identical to a sequence selected from the group consisting of SEQ ID NO: 36 and SEQ ID NO: 48.

17 . The nucleic acid of claim 1 , wherein the regulatory element sequence is at least 90% identical to a sequence selected from the group consisting of SEQ ID NO: 43 and SEQ ID NO: 55.

18 . The nucleic acid of claim 1 , wherein the regulatory element sequence is at least 90% identical to a sequence selected from the group consisting of SEQ ID NO: 46 and SEQ ID NO: 58.

19 . A vector comprising the nucleic acid of claim 1 .

20 . The vector of claim 19 , comprising the following genetic elements in a 5′ to 3′ direction:

the 5′-ITR comprising a TR L , a 5′-ITR spacer, a IR L ;

a promoter;

the regulatory element sequence;

a protein-coding sequence; and

the 3′-ITR comprising a IR R , a 3′-ITR spacer, a TR R .

21 . The vector of claim 20 , wherein the TR L comprises a sequence that is at least 90% identical to a reverse sequence or a reverse complementary sequence of SEQ ID NO: 61; wherein the 5′-ITR spacer comprises a sequence that is at least 90% identical to a reverse sequence or a reverse complementary sequence of SEQ ID NO: 62; wherein the IR L comprises a sequence that is at least 90% identical to a reverse sequence or a reverse complementary sequence of SEQ ID NO: 63; wherein the TR R comprises a sequence that is at least 90% identical to a reverse sequence or a reverse complementary sequence of SEQ ID NO: 64; and wherein the IR R comprises a sequence that is at least 90% identical to a reverse sequence or a reverse complementary sequence of SEQ ID NO: 65.

22 . A cell comprising the nucleic acid of claim 1 .

Assignments (2)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Apr 21, 2023
From: CHEN, JI; ZHANG, YU; WANG, JUNG-HAO; LI, YARONG; ZHAO, BIN; LIAN, DUJUAN; ZHANG, YUCHEN; HUANG, CUI; ZHANG, ZHENG; CAI, JIEXING
To: WUXI BIOLOGICS (SHANGHAI) CO., LTD.
Reel/Frame 063404/0063 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Apr 21, 2023
From: WUXI BIOLOGICS (SHANGHAI) CO., LTD.
To: WUXI BIOLOGICS IRELAND LIMITED
Reel/Frame 063404/0298 →
Priority Claims (2)
CN 202010102211.1 · Feb 19, 2020 · national
WO PCT/CN2020/081464 · Mar 26, 2020 · international
Continuity (1)
Related Publication 20230203530A1 · Jun 29, 2023
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