IP Library Patent Application 18417725
Patent Application
App. No. 18/417,725

METHODS FOR TREATING CHOLESTASIS

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Quick Facts
Patent No.
US None
App. No.
18/417,725
Abstract

Provided herein are methods for treating cholestasis in a subject having a liver disease. The method includes administering to the subject an Apical Sodium-dependent Bile Acid Transporter (ASBTI). More specifically, the present invention relates to methods for treating cholestasis in a subject where the method includes administering an ASBTI to a subject at a dose of at least 10 μg/kg/day.

Claims (22)

1 - 102 . (canceled)

103 . A method for treating progressive familial intrahepatic cholestasis (PFIC) in a subject in need of such treatment comprising administering to the subject maralixibat in an amount of from about 560 μg/kg/day to about 1400 μg/kg/day.

104 . The method of claim 103 , wherein maralixibat is administered in an amount of about 560 μg/kg/day.

105 . The method of claim 103 , wherein maralixibat is administered in an amount of about 1100 μg/kg/day.

106 . The method of claim 103 , wherein maralixibat is administered in an amount of about 1200 μg/kg/day.

107 . The method of claim 103 , wherein maralixibat is administered in an amount from about 10 mg/day to about 100 mg/day.

108 . The method of claim 107 , wherein maralixibat is administered in an amount from about 20 mg/day to about 80 mg/day.

109 . The method of claim 103 , wherein the PFIC is selected from PFIC type 1, PFIC type 2, and PFIC type 3.

110 . The method of claim 109 , wherein the PFIC is PFIC type 1.

111 . The method of claim 109 , wherein the PFIC is PFIC type 2.

112 . The method of claim 109 , wherein the PFIC is PFIC type 3.

113 . The method of claim 103 , wherein maralixibat is administered once daily (QD).

114 . The method of claim 103 , wherein maralixibat is administered twice daily (BID).

115 . The method of claim 103 , wherein maralixibat is administered for at least 18 weeks.

116 . The method of claim 103 , wherein maralixibat is administered for at least 2 years.

117 . The method of claim 103 , wherein maralixibat is administered for at least 3 years.

118 . The method of claim 103 , wherein the subject exhibits below normal height or weight prior to the administration of maralixibat.

119 . The method of claim 103 , wherein the subject experiences pruritus prior to the administration of maralixibat.

120 . The method of claim 103 , wherein the subject is a pediatric subject.

121 . The method of claim 103 , wherein the subject is at least 1 year of age.

122 . The method of claim 103 , wherein maralixibat is administered prior to ingestion of food.

123 . The method of claim 103 , wherein maralixibat is administered orally.

Assignments (4)
CHANGE OF ADDRESS Recorded Jun 10, 2024
From: MIRUM PHARMACEUTICALS, INC.
To: MIRUM PHARMACEUTICALS, INC.
Reel/Frame 067680/0956 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Jan 22, 2024
From: JAECKLIN, THOMAS
To: MIRUM PHARMACEUTICALS, INC.
Reel/Frame 066199/0923 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Jan 22, 2024
From: DORENBAUM, ALEJANDRO
To: SHIRE HUMAN GENETIC THERAPIES, INC.
Reel/Frame 066200/0126 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Jan 22, 2024
From: SHIRE HUMAN GENETIC THERAPIES, INC.
To: MIRUM PHARMACEUTICALS, INC.
Reel/Frame 066200/0241 →