IP Library Granted Patent US 9,908,899
Granted Patent B2
US 9,908,899 · App. 15/337,354 · Granted Mar 6, 2018

Histone deacetylase inhibitors

Inventors: Vincent Jacques (Somerville, MA); James R. Rusche (Framingham, MA); Norton P. Peet (North Andover, MA); Jasbir Singh (Naperville, IL)
Assignee: BIOMARIN PHARMACEUTICAL INC.
C07D513/04C07D205/06C07D211/70C07D211/78C07D231/12C07D261/08C07D263/32C07D277/30C07D277/34C07D305/10C07D401/06C07D403/06C07D403/10C07D451/02C07D471/04C07D471/08
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Quick Facts
Patent No.
US 9,908,899
App. No.
15/337,354
Granted
Mar 6, 2018
Kind
B2
Abstract

The compounds provided herein are phenyl analine amides and are useful for inhibiting histone deacteylase (“HDAC”) enzymes, such as HDAC1, HDAC2, and HDAC3.

Claims (38)

1. A method of inhibiting HDAC1, HDAC2, or HDAC3 in a subject, comprising administering to the subject an effective amount of a compound having a structure of formula (II):

wherein:

R A is H or F;

R C is H, Cl, or F;

Het is selected from oxetanyl, azetindinyl, piperidinyl, and 8-azabicyclo[3.2.1]octanyl, and when Het is azetindinyl, piperidinyl, or 8-azabicyclo[3.2.1]octanyl, the ring nitrogen is substituted with R B ; and

R B is C 1 -C 6 alkyl, C 1 -C 6 hydroxyalkyl, C 1 -C 3 alkylene-C 3 -C 6 cycloalkyl, C 1 -C 3 alkylene-phenyl, or C 1 -C 3 alkylene-pyridyl; wherein the phenyl or pyridyl ring is optionally substituted with methyl;

or a pharmaceutically acceptable salt thereof.

2. The method of claim 1 , wherein R A is H.

3. The method of claim 1 , wherein R A is F.

4. The method of claim 1 , wherein Het is oxetanyl.

5. The method of claim 1 , wherein Het is azetindinyl, piperidinyl, or 8-azabicyclo [3.2.1]octanyl.

6. The method of claim 1 , wherein Het is azetindinyl or piperidinyl.

7. The method of claim 1 , wherein R B is C 1-6 alkyl, C 1-6 hydroxyalkyl, CH 2 -cyclopropyl, CH 2 -phenyl, or CH 2 -pyridyl, and the pyridyl is optionally substituted with methyl.

8. The method of claim 1 , wherein R B is methyl, CH 2 C(CH 3 ) 3 , CH 2 C(CH 3 ) 2 OH, CH 2 -cyclopropyl, CH 2 -phenyl, CH 2 -pyridyl, or CH 2 -methylpyridyl.

9. The method of claim 1 , wherein Het is azetindinyl, piperidinyl, or 8-azabicyclo [3.2.1]octanyl; and R B is C 1-6 alkyl, C 1-6 hydroxyalkyl, CH 2 -cyclopropyl, CH 2 -phenyl, or CH 2 -pyridyl, or CH 2 -methylpyridyl.

10. The method of claim 9 , wherein Het is azetindinyl, and R B is C 1-6 alkyl, CH 2 C(CH 3 ) 2 OH, CH 2 -cyclopropyl, CH 2 -phenyl, or CH 2 -methylpyridyl.

11. The method of claim 9 , wherein Het is piperidinyl, and R B is C 1-6 alkyl, CH 2 C(CH 3 ) 2 OH, CH 2 -cyclopropyl, CH 2 -phenyl, CH 2 -pyridyl, or CH 2 -methylpyridyl.

12. The method of claim 9 , wherein Het is 8-azabicyclo [3.2.1]octanyl and R B is C 1-6 alkyl.

13. The method of claim 1 , wherein the subject suffers from a neurological disease.

14. The method of claim 13 , wherein the neurological disease is Friedreich's ataxia.

15. A method of treating a neurological disease or disorder selected from Friedreich's ataxia, myotonic dystrophy, spinal muscular atrophy, fragile X syndrome, Huntington's disease, spinocerebellar ataxia, Kennedy's disease, amyotrophic lateral sclerosis, spinal and bulbar muscular atrophy, and Alzheimer's disease; cutaneous T-cell lymphoma; a B cell lymphoma; colorectal cancer; psoriasis; rheumatoid arthritis; osteoarthritis; a long-term memory impairment condition; or a drug addiction in a subject in need thereof, the method comprising administering to the subject an effective amount of a compound having a structure of formula (II):

wherein:

R A is H or F;

R C is H, Cl, or F;

Het is selected from oxetanyl, azetindinyl, piperidinyl, and 8-azabicyclo[3.2.1]octanyl, and when Het is azetindinyl, piperidinyl, or 8-azabicyclo[3.2.1]octanyl, the ring nitrogen is substituted with R B ;

R B is C 1 -C 6 alkyl, C 1 -C 6 hydroxyalkyl, C 1 -C 3 alkylene-C 3 -C 6 cycloalkyl, C 1 -C 3 alkylene-phenyl, or C 1 -C 3 alkylene-pyridyl; wherein the phenyl or pyridyl ring is optionally substituted with methyl;

or a pharmaceutically acceptable salt thereof.

16. The method of claim 15 , wherein Het is azetindinyl, piperidinyl, or 8-azabicyclo [3.2.1]octanyl.

17. The method of claim 15 , wherein Het is azetindinyl or piperidinyl.

18. The method of claim 15 , wherein R B is C 1-6 alkyl, C 1-6 hydroxyalkyl, CH 2 -cyclopropyl, CH 2 -phenyl, or CH 2 -pyridyl, wherein the pyridyl is optionally substituted with methyl.

19. The method of claim 15 , wherein Het is azetindinyl, piperidinyl, or 8-azabicyclo [3.2.1]octanyl; and R B is C 1-6 alkyl, CH 2 C(CH 3 ) 2 OH, CH 2 -cyclopropyl, CH 2 -phenyl, or CH 2 -pyridyl, wherein the pyridyl is optionally substituted with methyl.

20. A method of treating a neurological disease or disorder selected from Friedreich's ataxia, myotonic dystrophy, spinal muscular atrophy, fragile X syndrome, Huntington's disease, spinocerebellar ataxia, Kennedy's disease, amyotrophic lateral sclerosis, spinal and bulbar muscular atrophy, and Alzheimer's disease; cutaneous T-cell lymphoma; a B cell lymphoma; colorectal cancer; psoriasis; rheumatoid arthritis; osteoarthritis; a long-term memory impairment condition; or a drug addiction in a subject in need thereof, the method comprising administering to the subject an effective amount of a compound selected from the group consisting of:

or a pharmaceutically acceptable salt thereof.

21. The method of claim 20 , wherein the disease or disorder is Friedreich's ataxia.

22. A method of inhibiting HDAC1, HDAC2, or HDAC3 in a subject, the method comprising administering to the subject an effective amount of a compound selected from the group consisting of:

or a pharmaceutically acceptable salt thereof.

23. The method of claim 22 , wherein the subject suffers from a neurological disease.

24. The method of claim 23 , wherein the neurological disease is Friedreich's ataxia.

Assignments (2)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Feb 8, 2017
From: JACQUES, VINCENT; RUSCHE, JAMES R.; PEET, NORTON P.; SINGH, JASBIR
To: REPLIGEN CORPORATION
Reel/Frame 041199/0638 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Feb 8, 2017
From: REPLIGEN CORPORATION
To: BIOMARIN PHARMACEUTICAL INC.
Reel/Frame 041199/0694 →
Continuity (5)
Continuation 14598583 · Jan 16, 2015
Continuation 13843261 · Mar 15, 2013
Continuation In Part PCTUS2012026874 · Feb 28, 2012
Provisional Application 61447416 · Feb 28, 2011
Related Publication 20170044186A1 · Feb 16, 2017