IP Library › Granted Patent US 12,427,124
Granted Patent B1
US 12,427,124 · App. 19/062,521 · Granted Sep 30, 2025

Phenylalanine-based LAT1 inhibitors and uses thereof

Inventors: Bernd Jandeleit (Menlo Park, CA); Guangyao Gao (Los Altos, CA); Wolf-Nicolas Fischer (Sunnyvale, CA); Gordon Ringold (Los Altos Hills, CA)
Assignee: Maxymune Therapeutics, Inc.
A61K31/145A61K31/10C07C311/33C07C311/39C07C311/43C07C311/44C07C317/14C07C2601/14C07C2601/16C07C2602/10
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Quick Facts
Patent No.
US 12,427,124
App. No.
19/062,521
Granted
Sep 30, 2025
Kind
B1
Abstract

Phenylalanine-based inhibitors of the Large Amino Acid Transporter 1 (LAT1) are disclosed. The compounds are useful in modulating the transcellular transport of substrates of LAT1 such as large neutral amino acids. The compounds are useful in immunomodulation therapies.

Claims (71)

1. A compound having the structure of Formula (3):

or a pharmaceutically acceptable salt thereof, wherein,

R 6 is selected from —COOH, —COOR a , —COR a , and —CON(R b ) 2 , wherein,

R a is C 1-4 alkyl; and

each R b is independently selected from hydrogen, —OH, C 1-4 alkyl, and C 1-4 alkoxy;

R 7 is selected from hydrogen and methyl;

R 8 is selected from hydrogen, halogen, C 1-3 alkyl, and C 1-3 alkoxy;

R 9 is selected from —S(O) 2 —NR— and —NR—S(O) 2 —, wherein R is selected from hydrogen and methyl;

R 10 is selected from C 6-10 aryl, substituted C 6-10 aryl, C 5-6 cycloalkyl, and biphenyl; and

each substituent is independently selected from halogen, phenyl, —N(—R) 2 , C 1-4 alkoxy, and C 1-4 alkyl, wherein each R is independently selected from hydrogen and methyl.

2. The compound of claim 1 , wherein R 6 is —COOH.

3. The compound of claim 1 , wherein R 7 is hydrogen.

4. The compound of claim 1 , wherein R 8 is methyl.

5. The compound of claim 1 , wherein R 9 is —S(O) 2 —NR—.

6. The compound of claim 1 , wherein R 9 is —NR—S(O) 2 —.

7. The compound of claim 1 , wherein R 9 is —S(O) 2 —NH—.

8. The compound of claim 1 , wherein R 9 is —NH—S(O) 2 —.

9. The compound of claim 1 , wherein R 10 is phenyl.

10. The compound of claim 1 , wherein R 10 is substituted phenyl.

11. The compound of claim 10 , wherein the substituted phenyl is 4-substituted phenyl.

12. The compound of claim 10 , wherein the substituted phenyl is 3-substituted phenyl.

13. The compound of claim 10 , wherein the substituent is selected from Cl, Br, methoxy, and benzyl.

14. The compound of claim 1 , wherein R 10 is naphthyl.

15. The compound of claim 1 , wherein R 10 is substituted naphthyl.

16. The compound of claim 15 , wherein the substituted naphthyl is 5-substituted naphthyl.

17. The compound of claim 15 , wherein the substituent is —N(R) 2 .

18. The compound of claim 15 , wherein the substituent is —N(—CH 3 ) 2 .

19. The compound of claim 1 , wherein R 10 is biphenyl.

20. The compound of claim 1 , wherein R 10 is cyclohexyl.

21. The compound of claim 1 , wherein

R 6 is —COOH;

R 7 is hydrogen;

R 8 is methyl; and

R 9 is —S(O) 2 —NH—.

22. The compound of claim 1 , wherein

R 6 is —COOH;

R 7 is hydrogen;

R 8 is methyl; and

R 9 is —NH—S(O) 2 —.

23. The compound of claim 1 , wherein the compound is selected from:

(S)-2-amino-3-(5-((5-(dimethylamino)naphthalene)-1-sulfonamido)-2-methylphenyl)propanoic acid (2);

(S)-2-amino-3-(3-((5-(dimethylamino)naphthalene)-1-sulfonamido)phenyl)propanoic acid (3);

(S)-2-amino-3-(2-methyl-5-((4-methylphenyl)sulfonamido)phenyl)propanoic acid (7);

(S)-2-amino-3-(2-methyl-5-(phenylsulfonamido)phenyl)propanoic acid (10);

(S)-2-amino-3-(5-((5-(dimethylamino)naphthalene)-1-sulfonamido)-2-isopropylphenyl)propanoic acid (21);

(S)-2-amino-3-(5-((3-bromophenyl)sulfonamido)-2-methylphenyl)propanoic acid (29);

(S)-2-amino-3-(5-(N-benzylsulfamoyl)-2-methylphenyl)propanoic acid (30);

(S)-2-amino-3-(2-methyl-5-(N-phenylsulfamoyl)phenyl)propanoic acid hydrochloride (35);

(S)-3-(5-([1,1′-biphenyl]-3-sulfonamido)-2-methylphenyl)-2-aminopropanoic acid (38);

(S)-2-amino-3-(2-methyl-5-(N-(naphthalen-1-yl)sulfamoyl)phenyl)propanoic acid (39);

(S)-3-(5-(N-([1,1′-biphenyl]-4-yl)sulfamoyl)-2-methylphenyl)-2-aminopropanoic acid (40);

(S)-2-amino-3-(5-((3,5-dichlorophenyl)sulfonamido)-2-methylphenyl)propanoic acid (43);

(S)-2-amino-3-(5-(N-(4-methoxyphenyl)sulfamoyl)-2-methylphenyl)propanoic acid (44);

(S)-2-amino-3-(5-(N-(5-(dimethylamino)naphthalen-1-yl)sulfamoyl)-2-methylphenyl)propanoic acid (49);

(S)-2-amino-3-(5-(N-(4-chlorophenyl)sulfamoyl)-2-methylphenyl)propanoic acid (52);

(S)-2-amino-3-(5-(N-cyclohexylsulfamoyl)-2-methylphenyl)propanoic acid (53);

(S)-2-amino-3-(5-((benzylthio)methyl)-2-methylphenyl)propanoic acid (55);

(S)-2-amino-3-(5-(benzylsulfonyl)-2-methylphenyl)propanoic acid (65);

(S)-2-amino-3-(5-(N-(3-bromophenyl)sulfamoyl)-2-methylphenyl)propanoic acid (76);

(S)-2-amino-3-(5-(N-(4-bromophenyl)sulfamoyl)-2-methylphenyl)propanoic acid (77);

(S)-2-amino-3-(3-(N-(4-chlorophenyl)sulfamoyl)phenyl)propanoic acid (79);

tert-butyl (S)-2-amino-3-(5-(N-(4-chlorophenyl)sulfamoyl)-2-methylphenyl)propanoate (82);

(S)-2-amino-3-(5-(N-(4-chlorophenyl)-N-methylsulfamoyl)-2-methylphenyl)propanoic acid (84);

(S)-2-amino-3-(5-(N-(4-chlorophenyl)sulfamoyl)-2-isopropylphenyl)propanoic acid (86); and

(S)-2-amino-3-(5-((4-(tert-butyl)phenyl)sulfonamido)-2-methylphenyl)propanoic acid (87);

or a pharmaceutically acceptable salt of any of the foregoing.

24. A pharmaceutical composition comprising the compound of claim 1 or a pharmaceutically acceptable salt thereof; and a pharmaceutically acceptable vehicle.

25. A method of treating an organ transplant rejection, an acute graft-vs-host-disease, or a chronic graft-vs-host-disease in a patient comprising administering to a patient in need of such treatment a therapeutically effective amount of the compound of claim 1 or a pharmaceutically acceptable salt thereof.

26. A method of treating a disease in a patient comprising administering to a patient in need of such treatment a therapeutically effective amount of the compound of claim 1 or a pharmaceutically acceptable salt thereof, wherein the disease is selected from alopecia, pemphigus, psoriasis, scleroderma, vitiligo, dermatitis, asthma, fibrosis, rheumatoid arthritis, lupus, Crohn's disease, ulcerative colitis, and Celiac disease.

27. A method of treating an organ transplant rejection, an acute graft-vs-host-disease, or a chronic graft-vs-host-disease in a patient comprising administering to a patient in need of such treatment a therapeutically effective amount of the pharmaceutical composition of claim 24 .

28. A method of treating a disease in a patient comprising administering to a patient in need of such treatment a therapeutically effective amount of the pharmaceutical composition of claim 24 , wherein the disease is selected from alopecia, pemphigus, psoriasis, scleroderma, vitiligo, dermatitis, asthma, fibrosis, rheumatoid arthritis, lupus, Crohn's disease, ulcerative colitis, and Celiac disease.

Assignments (1)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Mar 4, 2025
From: JANDELEIT, BERND; GAO, GUANGYAO; FISCHER, WOLF-NICOLAS; RINGOLD, GORDON
To: MAXYMUNE THERAPEUTICS, INC.
Reel/Frame 070394/0768 →
Continuity (2)
Provisional Application 63746489 · Jan 17, 2025
Provisional Application 63632130 · Apr 10, 2024
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