IP Library Granted Patent US 11,060,107
Granted Patent B2
US 11,060,107 · App. 15/664,036 · Granted Jul 13, 2021

Purification and purity assessment of RNA molecules synthesized with modified nucleosides

Inventors: Drew Weissman (Wynnewood, PA); Katalin Kariko (Rydal, PA)
Assignee: The Trustees of the University of Pennsylvania
C12N15/85C07H21/02C07K14/475C07K14/505C07K14/52C12P19/34A61K48/00C12N2310/335C12N2320/30
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Quick Facts
Patent No.
US 11,060,107
App. No.
15/664,036
Granted
Jul 13, 2021
Kind
B2
Abstract

This invention provides purified preparations of an RNA, oligoribonucleotide, or polyribonucleotide comprising a modified nucleoside, and methods of assessing purity of purified preparations of an RNA, oligoribonucleotide, or polyribonucleotide comprising a modified nucleoside.

Claims (7)

1. A purified preparation of RNA, the RNA comprising at least one modified nucleoside selected from the group consisting of a 1-methyl-pseudouridine, m5C, m5U, m6A, s2U, Ψ, and 2′-O-methyl-U, wherein about 95% to about 99.9% of RNA in the purified preparation is messenger RNA, and wherein the purified preparation is prepared by subjecting a preparation of messenger RNA to enzymatic digestion with 0.001 units of at least one enzyme selected from the group consisting of RNase III, RNase V1, Dicer, and Chipper.

2. The purified preparation of RNA of claim 1 , whereby the RNA is significantly less immunogenic than an unpurified preparation of RNA with the same sequence.

3. A purified preparation of RNA, the RNA comprising at least one modified nucleoside selected from the group consisting of a 1-methyl-pseudouridine, m5C, m5U, m6A, s2U, Ψ, and 2′-O-methyl-U, wherein about 95% to about 99.9% of RNA in the purified preparation is messenger RNA, and wherein the purified preparation is prepared by subjecting a preparation of messenger RNA to liquid chromatography using a linear gradient of 38% Buffer B (0.1 M triethylammonium acetate, 25% acetonitrile, pH 7.0) to 55% Buffer B in Buffer A (0.1 M triethylammonium acetate, pH 7.0) over 22 minutes.

4. The purified preparation of RNA of claim 3 , whereby the RNA is significantly less immunogenic than an unpurified preparation of RNA with the same sequence.

5. The purified preparation of RNA of claim 1 , wherein the purified preparation is substantially free of double stranded RNA contaminants.

6. The purified preparation of RNA of claim 3 , wherein the purified preparation is substantially free of double stranded RNA contaminants.

7. The purified preparation of RNA of claim 1 , wherein said enzymatic digestion occurs at 37° for about 15-120 minutes in about 33-200 mM acetate buffer at a pH of about 7.5-8.0.

Assignments (1)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded May 10, 2019
From: WEISSMAN, DREW; KARIKO, KATALIN
To: THE TRUSTEES OF THE UNIVERSITY OF PENNSYLVANIA
Reel/Frame 049138/0481 →
Continuity (3)
Continuation 14776525
Provisional Application 61783645 · Mar 14, 2013
Related Publication 20170327842A1 · Nov 16, 2017
Cited By (4)
US 12,186,389 US 12,194,089 US 12,390,523 US 12,570,725