IP Library › Granted Patent US 11,607,408
Granted Patent B2
US 11,607,408 · App. 17/070,622 · Granted Mar 21, 2023

Method of treatment of schizophrenia

Inventors: Sandra Smieszek (Cleveland, OH); Mihael H. Polymeropoulos (Potomac, MD)
Assignee: Vanda Pharmaceuticals Inc.
A61K31/454A61K31/451A61K31/5415A61K45/06A61P25/18
View Patent ↗
Loading inventors, assignments & file history…
Monitor This Case
Get email alerts when status or documents change.
Order Certified Copies
Most orders are placed with the USPTO same day — all within 24 business hours.
Order via The Patent Place →
Pre-filled with this patent's details
Quick Facts
Patent No.
US 11,607,408
App. No.
17/070,622
Granted
Mar 21, 2023
Kind
B2
Abstract

The invention relates generally to improvements in the treatment of psychotic symptoms, and more particularly, to improvements in the identification of an individual or a population of individuals for whom treatment with iloperidone, an iloperidone metabolite, or pharmaceutically-acceptable salts thereof may provide a particular benefit in treating an individual's psychotic symptoms based on the individual's genotype at the PPEF2 locus.

Claims (50)

1. In a method consisting of administering to a schizophrenia patient an amount of an active pharmaceutical ingredient (API) effective to treat said patient's schizophrenia, wherein the API is iloperidone, a metabolite of iloperidone, or a pharmaceutically acceptable salt of iloperidone or the metabolite thereof, the improvement comprising:

selecting said patient for treatment based upon a determination that said patient's gene sequence includes a mutation in PPEF2.

2. The improvement of claim 1 , in which the mutation in PPEF2 is a loss of function mutation.

3. The improvement of claim 1 , in which the mutation in PPEF2 is a missense mutation that is R86H.

4. The improvement of claim 1 , wherein the mutation is a stopgain mutation that is PPEF2:NM 006239:exon3:c.G135A:p.W45X.

5. The improvement of claim 1 , wherein the API is iloperidone, and the amount of iloperidone is 12 mg/day to 24 mg/day.

6. A method for treating a schizophrenia patient, comprising:

identifying the patient's genotype at the PPEF2 locus; and

if the patient has a genotype including a mutation in PPEF2, then internally administering an active pharmaceutical ingredient (API) to the patient, wherein the API is iloperidone, a metabolite of iloperidone, or a pharmaceutically acceptable salt of iloperidone or the metabolite thereof.

7. The method of claim 6 , in which the mutation in PPEF2 is a loss of function mutation.

8. The method of claim 6 , in which the mutation in PPEF2 is a missense mutation, and wherein the missense mutation in PPEF2 is R86H.

9. The method of claim 6 , wherein the mutation is a stopgain mutation, and wherein the stopgain mutation is PPEF2:NM_006239:exon3:c.G135A:p.W45X.

10. The method according to claim 6 , wherein the step of identifying comprises:

obtaining or having obtained a biological sample from the patient; and

performing or having performed a genotyping assay on the biological sample to determine the patient's PPEF2 genotype.

11. In a method consisting of administering to a schizophrenia patient an amount of an active pharmaceutical ingredient (API) effective to treat said patient's schizophrenia, the improvement comprising:

selecting said patient for treatment based upon a determination that said patient's gene sequence includes a loss of function mutation in PPEF2.

12. The improvement of claim 11 , wherein the API comprises:

a) an atypical antipsychotic agent, wherein the atypical antipsychotic agent is selected from the group consisting of: aripiprazole, asenapine, clozapine, iloperidone, a metabolite of iloperidone, a pharmaceutically acceptable salt of iloperidone, a pharmaceutically acceptable salt of the metabolite of iloperidone, lurasidone, olanzapine, paliperidone, quetiapine, risperidone, and ziprasidone;

b) a typical antipsychotic agent, wherein the typical antipsychotic agent is selected from the group consisting of: chlorpromazine, fluphenazine, haloperidol, perphenazine, thioridazine, and thiothixene; or

c) an mGluR5 agonist.

13. The improvement of claim 11 , wherein the API is iloperidone, and the amount of iloperidone is 12 mg/day to 24 mg/day.

14. In a method consisting of administering to a schizophrenia patient an amount of an active pharmaceutical ingredient (API) effective to treat said patient's schizophrenia, the improvement comprising:

selecting said patient for treatment based upon a determination that said patient's gene sequence includes a stopgain mutation in PPEF2.

15. The improvement of claim 14 , wherein the stopgain mutation is PPEF2:NM_006239:exon3:c.G135A:p.W45X.

16. The improvement of claim 14 , wherein the API comprises:

a) an atypical antipsychotic agent, wherein the atypical antipsychotic agent is selected from the group consisting of: aripiprazole, asenapine, clozapine, iloperidone, a metabolite of iloperidone, a pharmaceutically acceptable salt of iloperidone, a pharmaceutically acceptable salt of the metabolite of iloperidone, lurasidone, olanzapine, paliperidone, quetiapine, risperidone, and ziprasidone;

b) a typical antipsychotic agent, wherein the typical antipsychotic agent is selected from the group consisting of: chlorpromazine, fluphenazine, haloperidol, perphenazine, thioridazine, and thiothixene; or

c) an mGluR5 agonist.

17. The improvement of claim 14 , wherein the API is iloperidone, and the amount of iloperidone is 12 mg/day to 24 mg/day.

18. A method for treating a schizophrenia patient, comprising:

identifying the patient's genotype at the PPEF2 locus; and

if the patient has a genotype including a loss of function mutation in PPEF2, then internally administering an active pharmaceutical ingredient (API) to the patient.

19. The method of claim 18 , wherein the API comprises:

a) an atypical antipsychotic agent, wherein the atypical antipsychotic agent is selected from the group consisting of: aripiprazole, asenapine, clozapine, iloperidone, a metabolite of iloperidone, a pharmaceutically acceptable salt of iloperidone, a pharmaceutically acceptable salt of the metabolite of iloperidone, lurasidone, olanzapine, paliperidone, quetiapine, risperidone, and ziprasidone;

b) a typical antipsychotic agent, wherein the typical antipsychotic agent is selected from the group consisting of: chlorpromazine, fluphenazine, haloperidol, perphenazine, thioridazine, and thiothixene; or

c) an mGluR5 agonist.

20. The method according to claim 18 , wherein the step of identifying comprises:

obtaining or having obtained a biological sample from the patient; and

performing or having performed a genotyping assay on the biological sample to determine the patient's PPEF2 genotype.

21. A method for treating a schizophrenia patient, comprising:

identifying the patient's genotype at the PPEF2 locus; and

if the patient has a genotype including a stopgain mutation in PPEF2, then internally administering an active pharmaceutical ingredient (API) to the patient.

22. The method of claim 21 , wherein the API comprises:

a) an atypical antipsychotic agent, wherein the atypical antipsychotic agent is selected from the group consisting of: aripiprazole, asenapine, clozapine, iloperidone, a metabolite of iloperidone, a pharmaceutically acceptable salt of iloperidone, a pharmaceutically acceptable salt of the metabolite of iloperidone, lurasidone, olanzapine, paliperidone, quetiapine, risperidone, and ziprasidone;

b) a typical antipsychotic agent, wherein the typical antipsychotic agent is selected from the group consisting of: chlorpromazine, fluphenazine, haloperidol, perphenazine, thioridazine, and thiothixene; or

c) an mGluR5 agonist.

23. The method according to claim 21 , wherein the step of identifying comprises:

obtaining or having obtained a biological sample from the patient; and

performing or having performed a genotyping assay on the biological sample to determine the patient's PPEF2 genotype.

Assignments (1)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Oct 15, 2020
From: SMIESZEK, SANDRA; POLYMEROPOULOS, MIHAEL H.
To: VANDA PHARMACEUTICALS INC.
Reel/Frame 054067/0837 →
Continuity (2)
Provisional Application 62915395 · Oct 15, 2019
Related Publication 20210106575A1 · Apr 15, 2021
Cited By (1)
US 12,606,869