IP Library Granted Patent US 11,873,300
Granted Patent B2
US 11,873,300 · App. 16/992,441 · Granted Jan 16, 2024

Crystalline forms of CFTR modulators

Inventors: Yi Shi (Natick, MA); Kevin J. Gagnon (Acton, MA); Jicong Li (Cambridge, MA); Jennifer Lu (San Diego, CA); Ales Medek (Winchester, MA); Muna Shrestha (Belmont, MA); Michael Waldo (Grafton, MA); Beili Zhang (San Diego, CA); Carl L. Zwicker (Wakefield, MA); Corey Don Anderson (Brighton, MA); Jeremy J. Clemens (San Diego, CA); Thomas Cleveland (San Marcos, CA); Timothy Richard Coon (Carlsbad, CA); Bryan Frieman (La Jolla, CA); Peter Grootenhuis (Del Mar, CA); Sara Sabina Hadida Ruah (La Jolla, CA); Jason McCartney (Cardiff by the Sea, CA); Mark Thomas Miller (Rancho Santa Fe, CA); Prasuna Paraselli (San Diego, CA); Fabrice Pierre (La Jolla, CA); Sara E. Swift (San Diego, CA); Jinglan Zhou (San Diego, CA)
Assignee: Vertex Pharmaceuticals Incorporated
C07D471/08C07B2200/13
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Quick Facts
Patent No.
US 11,873,300
App. No.
16/992,441
Granted
Jan 16, 2024
Kind
B2
Abstract

Crystalline forms of Compound I: pharmaceutically acceptable salts thereof, and solvates and hydrates thereof are disclosed. Pharmaceutical compositions comprising the same, methods of treating cystic fibrosis using the same, and methods for making the same are also disclosed.

Claims (46)

1. Compound I calcium salt hydrate Form D

2. A pharmaceutical composition comprising the compound according to claim 1 .

3. The pharmaceutical composition according to claim 2 , further comprising one or more additional CFTR modulating compounds.

4. The pharmaceutical composition according to claim 3 , wherein at least one additional CFTR modulating compound is a CFTR potentiator.

5. The pharmaceutical composition according to claim 3 , wherein at least one additional CFTR modulating compound is a CFTR corrector.

6. The pharmaceutical composition according to claim 3 , wherein the one or more additional CFTR modulating compounds are selected from:

(a) Compound II:

7. A method of treating cystic fibrosis comprising administering the Compound I calcium salt hydrate Form D

to a subject in need thereof.

8. The method of treating cystic fibrosis according to claim 7 , wherein the Compound I calcium salt hydrate Form D is administered with one or more additional CFTR modulating compounds.

9. The method of treating cystic fibrosis according to claim 8 , wherein the one or more additional CFTR modulating compound are selected from:

10. A method of preparing Compound I calcium salt hydrate Form D according to claim 1 , comprising

(a) charging Compound I calcium salt hydrate Form A with EtOH/water.

(b) heating to 65° C., and

(c) isolating the resulting solids,

to provide Compound I calcium salt hydrate Form D.

11. The Compound I calcium salt hydrate Form D

characterized by an X-ray powder diffractogram (XRPD) having signals at 6.1±0.2 degrees two-theta, 16.2±0.2 degrees two-theta, and 22.8±0.2 degrees two-theta.

12. The Compound I calcium salt hydrate Form D of claim 11 , characterized by an XRPD having (a) signals at 6.1±0.2 degrees two-theta, 16.2±0.2 degrees two-theta, and 22.8±0.2 degrees two-theta; and (b) one or more signals selected from 5.5±0.2 degrees two-theta, 15.5±0.2 degrees two-theta, 19.7±0.2 degrees two-theta, 21.5±0.2 degrees two-theta, 22.1±0.2 degrees two-theta, 23.0±0.2 degrees two-theta, and 27.6±0.2 degrees two-theta.

13. Compound I calcium salt hydrate Form D of claim 11 , characterized by an XRPD having signals at 6.1±0.2 degrees two-theta, 16.2±0.2 degrees two-theta, and 22.8±0.2 degrees two-theta, and 27.6±0.2 degrees two-theta.

14. The Compound I calcium salt hydrate Form D of claim 11 , characterized by an XRPD having signals at 6.1±0.2 degrees two-theta, 15.5±0.2 degrees two-theta, 16.2±0.2 degrees two-theta, 19.7±0.2 degrees two-theta, 22.8±0.2 degrees two-theta, and 27.6±0.2 degrees two-theta.

15. The Compound I calcium salt hydrate Form D of claim 1 , characterized by an X-ray powder diffractogram substantially similar to FIG. 13 .

16. The Compound I calcium salt hydrate Form D

characterized by a triclinic crystal system, a P1 space group, and unit cell dimensions measured at 100 K on a Bruker diffractometer equipped with Cμ Kα radiation (λ=1.5478 Å) of

a

12.78 ± .01 Å

α

64.93 ± .02º

b

16.64 ± .01 Å

β

75.10 ± .02º

c

18.19 ± .01 Å

γ

 68.22 ± .02º.

17. The Compound I calcium salt hydrate Form D

characterized by a 13 C solid state nuclear magnetic resonance ( 13 C ss NMR) spectrum with one or more peaks selected from 130.2±0.2 ppm, 125.6±0.2 ppm, and 35.0±0.2 ppm.

18. The substantially crystalline Compound I calcium salt hydrate Form D of claim 17 , characterized by a 13 C ssNMR spectrum with one or more peaks selected from 179.8±0.2 ppm, 130.2±0.2 ppm, 125.6±0.2 ppm, 120.9±0.2 ppm, 55.2±0.2 ppm, 44.3±0.2 ppm, 35.0±0.2 ppm, and 1.6±0.2 ppm.

19. The Compound I calcium salt hydrate Form D of claim 17 , characterized by a 13 C ssNMR spectrum with (a) one or more peaks selected from 130.2±0.2 ppm, 125.6±0.2 ppm, and 35.0±0.2 ppm; and (b) one or more peaks selected from 176.9±0.2 ppm, 160.9±0.2 ppm, 142.0±0.2 ppm, and 98.6±0.2 ppm.

20. The Compound I calcium salt hydrate Form D of claim 1 , characterized by a 13 C ssNMR spectrum substantially similar to FIG. 14 .

21. The pharmaceutical composition according to claim 2 , wherein at least 85% of the Compound I is Compound I calcium salt hydrate Form D.

22. The pharmaceutical composition according to claim 2 , wherein at least 95% of the Compound I is Compound I calcium salt hydrate Form D.

23. A pharmaceutical composition comprising Compound I and a pharmaceutically acceptable carrier, wherein the Compound I comprises Compound I calcium salt hydrate Form D

24. The composition according to claim 23 , wherein at least 85% of the Compound I is Compound I calcium salt hydrate Form D.

25. The composition according to claim 23 , wherein at least 95% of the Compound I is Compound I calcium salt hydrate Form D.

Assignments (4)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Jul 26, 2021
From: SHI, YI; GAGNON, KEVIN J.; LI, JICONG; LU, JENNIFER; MEDEK, ALES; SHRESTHA, MUNA; WALDO, MICHAEL; ZWICKER, CARL L.; ANDERSON, COREY DON; MCCARTNEY, JASON; PARASELLI, PRASUNA; PIERRE, FABRICE; SWIFT, SARA E.
To: VERTEX PHARMACEUTICALS INCORPORATED
Reel/Frame 056976/0068 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Jul 26, 2021
From: GROOTENHUIS, PETER
To: VERTEX PHARMACEUTIALS (SAN DIEGO) LLC
Reel/Frame 056976/0088 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Jul 26, 2021
From: VERTEX PHARMACEUTICALS (SAN DIEGO) LLC
To: VERTEX PHARMACEUTICALS INCORPORATED
Reel/Frame 056976/0099 →
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Jul 26, 2021
From: ZHANG, BEILI; CLEMENS, JEREMY J.; CLEVELAND, THOMAS; COON, TIMOTHY RICHARD; FRIEMAN, BRYAN; HADIDA RUAH, SARA SABINA; MILLER, MARK THOMAS; ZHOU, JINGLAN
To: VERTEX PHARMACEUTICALS (SAN DIEGO) LLC
Reel/Frame 056976/0105 →
Continuity (3)
Provisional Application 62886565 · Aug 14, 2019
Provisional Application 63015903 · Apr 27, 2020
Related Publication 20210047323A1 · Feb 18, 2021
Cited By (5)
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