IP Library › Granted Patent US 12,653,838
Granted Patent B2
US 12,653,838 · App. 18/200,812 · Granted Jun 16, 2026

Methods of otoprotection against platinum-based antineoplastic agents

Inventors: John Lee (Arlington, MA); John R. Soglia (Sherborn, MA); Qi-Ying Hu (Needham, MA); Fuxin Shi (Winchester, MA)
Assignee: Decibel Therapeutics, Inc.
A61K33/04A61K9/0004A61K9/0046A61P27/16A61K33/243A61K47/36
View Patent ↗
Loading inventors, assignments & file history…
Monitor This Case
Get email alerts when status or documents change.
Order Certified Copies
Most orders are placed with the USPTO same day — all within 24 business hours.
Order via The Patent Place →
Pre-filled with this patent's details
Quick Facts
Patent No.
US 12,653,838
App. No.
18/200,812
Granted
Jun 16, 2026
Kind
B2
Abstract

Disclosed herein are methods for otoprotection against platinum-based antineoplastic agents by administering a thiosulfate salt to a subject in need thereof. Typically, the thiosulfate salt is administered to the subject scheduled to be administered a platinum-based antineoplastic agent within 4 hours. Alternatively, the thiosulfate salt is administered within 7 hours after the administration of a platinum-based neoplastic agent.

Claims (23)

1 . A method of mitigating platinum-induced hearing loss in a human subject in need thereof, the method comprising (i) administering to the subject by intratympanically or transtympanically injecting an effective amount of a hypertonic composition having a calculated osmolarity of 3,000-7,000 mOsm/L and comprising 0.5M-1.0M of a thiosulfate salt, wherein the calculated osmolarity is calculated based on the thiosulfate salt and an optional tonicity agent, if present, and (ii) intravenously administering platinum-based antineoplastic agent to the subject 1 to 3 hours following step (i).

2 . The method of claim 1 , wherein the thiosulfate salt is an alkaline thiosulfate salt, ammonium thiosulfate salt, or a solvate thereof.

3 . The method of claim 1 , wherein the thiosulfate salt is sodium thiosulfate.

4 . The method of claim 1 , wherein the hypertonic composition comprises 1.0M of the thiosulfate salt.

5 . The method of claim 1 , wherein the hypertonic composition additionally comprises 1%-2% (w/v) of hyaluronan.

6 . The method of claim 5 , wherein the hypertonic composition comprises 1% (w/v) of hyaluronan.

7 . The method of claim 1 , wherein 200-1,000 μL of the hypertonic pharmaceutical composition are administered to a round window of the human subject.

8 . The method of claim 1 , wherein the effective amount is an amount that produces a plasma thiosulfate concentration that is 30 UM or less at the time the platinum-based antineoplastic agent is administered.

9 . The method of claim 1 , wherein the effective amount is an amount that produces a maximum thiosulfate concentration of 0.6-10 mmol/L by 1 hour post administration.

10 . The method of claim 1 , wherein the effective amount is an amount that produces a thiosulfate concentration of 0.1-2 mmol/L by 7 hours post administration in the subject's cochlea.

11 . The method of claim 1 , wherein the hypertonic composition produces a cochlear thiosulfate C max that is at least 30 times greater than a cochlear C max of the platinum-based antineoplastic agent, wherein the cochlear C max concentrations are modeled by a pharmacokinetic simulation of intravenous infusion in a two compartment model.

12 . The method of claim 1 , wherein the hypertonic composition is administered transtympanically.

13 . The method of claim 12 , wherein the transtympanic administration is by injection directly through a tympanic membrane.

14 . The method of claim 13 , wherein prior to injection a separate ventilation hole in the tympanic membrane is created to allow air to escape the middle ear space.

15 . The method of claim 1 , wherein the thiosulfate salt is sodium thiosulfate, wherein the hypertonic composition comprises 1.0M of the thiosulfate salt, and wherein the hypertonic composition additionally comprises 1% (w/v) of hyaluronan.

16 . A hypertonic pharmaceutical composition having a calculated osmolarity of 400-1,500 mOsm/L and comprising 0.1 to 0.5M of an anti-platinum chemoprotectant agent, a liquid solvent, 5% to 20% (w/v) of a gelling agent relative to the liquid solvent, and an optional tonicity agent, wherein the calculated osmolarity is calculated based on the chemoprotectant agent and the tonicity agent, if present.

17 . A method for determining a treatment window for intratympanic or transtympanic administration of a hypertonic composition comprising 0.5M-1.0M of a thiosulfate salt, the method comprising:

a) providing a subject administered a hypertonic pharmaceutical composition comprising a thiosulfate salt by transtympanic or intratympanic injection;

b) obtaining a perilymph sample from the subject;

c) quantifying the concentration of thiosulfate salt in the perilymph sample using liquid chromatography with tandem mass spectrometry (LC-MS/MS);

d) intravenously administering a platinum-based antineoplastic agent to the subject;

e) repeating steps b) and c) one or more times; and

f) calculating the half-life of thiosulfate in the perilymph.

Assignments (1)
ASSIGNMENT OF ASSIGNOR'S INTEREST Recorded Jan 25, 2024
From: LEE, JOHN; SOGLIA, JOHN R.; HU, QI-YING; SHI, FUXIN
To: DECIBEL THERAPEUTICS, INC.
Reel/Frame 066242/0277 →
Continuity (4)
Continuation 17080326 · Oct 26, 2020
Continuation 16427567 · May 31, 2019
Related Publication 20240131055A1 · Apr 25, 2024
Related Publication 20240226141A9 · Jul 11, 2024
References Cited (81)
US 6497902B1 · Ma · 2002 [cited by applicant]
US 6649621B2 · Kopke et al. · 2003 [cited by applicant]
US 7790699B2 · Melvik et al. · 2010 [cited by applicant]
US 8496957B2 · Lichter et al. · 2013 [cited by applicant]
US 8496973B2 · Sherman et al. · 2013 [cited by applicant]
US 8784870B2 · Lichter et al. · 2014 [cited by applicant]
US 9427472B2 · Lichter et al. · 2016 [cited by applicant]
US 9944524B2 · Sherman et al. · 2018 [cited by applicant]
US 10272034B2 · Lichter et al. · 2019 [cited by applicant]
US 10596190B2 · Neuwelt · 2020 [cited by applicant]
US 10709732B2 · Hu · 2020 [cited by examiner]
US 10813947B1 · Lee · 2020 [cited by examiner]
US 11071751B2 · Hu · 2021 [cited by examiner]
US 11142456B2 · Sherman et al. · 2021 [cited by applicant]
US 11617793B2 · Lovelace et al. · 2023 [cited by applicant]
US 11690870B2 · Lee · 2023 [cited by examiner]
US 11857567B2 · Hu · 2024 [cited by examiner]
US 11964018B2 · Smith · 2024 [cited by applicant]
US 12311026B2 · Smith et al. · 2025 [cited by applicant]
US 20040186172A1 · Ibrahim · 2004 [cited by applicant]
US 20100273852A1 · Iinuma et al. · 2010 [cited by applicant]
US 20130045957A1 · Piu et al. · 2013 [cited by applicant]
US 20130085476A1 · Imran · 2013 [cited by applicant]
US 20170182089A1 · Neuwelt et al. · 2017 [cited by applicant]
US 20180000950A1 · Savel et al. · 2018 [cited by applicant]
US 20180161297A1 · Kirnon et al. · 2018 [cited by applicant]
US 20180228903A1 · Kohane et al. · 2018 [cited by applicant]
US 20180360874A1 · Nivoliez · 2018 [cited by applicant]
US 20190144276A1 · Sherman et al. · 2019 [cited by applicant]
US 20190160094A1 · Neuwelt · 2019 [cited by applicant]
US 20190192425A1 · Lichter et al. · 2019 [cited by applicant]
US 20190210107A1 · Palmer · 2019 [cited by applicant]
US 20190336524A1 · Hu et al. · 2019 [cited by applicant]
US 20200009255A1 · Lovelace et al. · 2020 [cited by applicant]
US 20200023003A1 · Lee et al. · 2020 [cited by applicant]
US 20200038436A1 · Neuwelt · 2020 [cited by applicant]
US 20200338119A1 · Hu et al. · 2020 [cited by applicant]
US 20210308176A1 · Hu et al. · 2021 [cited by applicant]
US 20220063999A1 · Sherman et al. · 2022 [cited by applicant]
CA 2767168A1 · 2011 [cited by applicant]
EP 3570826A4 · 2019 [cited by applicant]
WO WO2007038949A1 · 2007 [cited by applicant]
WO WO2017139684A1 · 2017 [cited by applicant]
WO WO2018136605A1 · 2018 [cited by applicant]
WO WO2019108592A2 · 2019 [cited by applicant]
WO WO2019118330A1 · 2019 [cited by applicant]
WO WO2019126783A1 · 2019 [cited by applicant]
WO WO2019140012A1 · 2019 [cited by applicant]
WO WO2019154895A1 · 2019 [cited by applicant]
WO WO2019157370A1 · 2019 [cited by applicant]
WO WO2019210107A1 · 2019 [cited by applicant]
WO WO2019244121A1 · 2019 [cited by applicant]
WO WO2020256548A1 · 2020 [cited by applicant]
Schroeder, R.J., Audlin, J., Luo, J., Nicholas, B.D. “Pharmacokinetics of sodium thiosulfate in guinea pig perilymph following middle ear application” Journal of Otology. 2018. 13 p. 54-58. (Year: 2018). [cited by examiner]
Sargent, M. “Guide to achieving reliable quantitative LC-MS measurements” RSC Analytical Methods Committee. 2013. p. i-68. (Year: 2013). [cited by examiner]
“Cisplatin With or Without Sodium Thiosulfate in Treating Young Patients With Stage I, II, or III Childhood Liver Cancer (SIOPEL 6),” US National Library of Medicine, <https://clinicaltrials.gov/ct2/show/study/NCT006521… [cited by applicant]
“Efficacy of Trans-tympanic Injections of a Sodium Thiosulfate Gel to Prevent Cisplatin-induced Ototoxicity (STS001),” U.S. National Library of Medicine, <https://clinicaltrials.gov/ct2/show/NCT02281006?term=thiosulfate… [cited by applicant]
“Investigation of Hyaluronic Acid With Sustained Drug Release Effect for Inner Ear DDS.” Audiology Japan. 56(5):473-474 (2013) (4 pages). [cited by applicant]
Andersson et al., “Pharmacokinetics of cisplatin and its monohydrated complex in humans,” J Pharm Sci. 85(8):824-7 (1996). [cited by applicant]
Berglin et al., “Prevention of cisplatin-induced hearing loss by administration of a thiosulfate-containing gel to the middle ear in a guinea pig model,” Cancer Chemother Pharmacol. 68(6):1547-56 (2011). [cited by applicant]
Brock et al., “Sodium Thiosulfate for Protection from Cisplatin-Induced Hearing Loss,” N Engl J Med. 378(25): 2376-85 (Jun. 2018). [cited by applicant]
Choi et al., “Perilymph osmolality modulates cochlear function,” available in PMC Mar. 14, 2013, published in final edited form as: Laryngoscope. 118(9):1621-9 (2008) (16 pages). [cited by applicant]
Dillard et al., “Global burden of ototoxic hearing loss associated with platinum-based cancer treatment: A systematic review and meta-analysis,” Cancer Epidemiol. 79:102203 (Aug. 2022) (10 pages). [cited by applicant]
Freyer et al., “Interventions for cisplatin-induced hearing loss in children and adolescents with cancer,” Lancet Child Adolesc Health. doi: 10.1016/S2352-4642(19)30115-4 (May 2019) (7 pages). [cited by applicant]
International Search Report and Written Opinion for International Application No. PCT/US2020/035271, mailed Jul. 2, 2020 (18 pages). [cited by applicant]
Johnsson et al., “Pharmacokinetics and tissue distribution of cisplatin in nude mice: platinum levels and cisplatin-DNA adducts,” Cancer Chemother Pharmacol. 37(1-2):23-31 (1995). [cited by applicant]
Khunmanee et al., “Crosslinking method of hyaluronic-based hydrogel for biomedical applications,” J Tissue Eng. 8:1-16 (2017). [cited by applicant]
Leitao et al., “Quantification of sodium thiosulphate protection on cisplatin-induced toxicities,” J Otolaryngol. 32(3):146-50 (2003). [cited by applicant]
Meyer et al., “Randomized controlled trial to test the efficacy of transtympanic injections of a sodium thiosulfate gel to prevent cisplatin-induced ototoxicity,” J Clin Oncol. 35(15): Supp. Supplement 1 (2017) (Abstrac… [cited by applicant]
Muldoon et al., “Delayed Administration of Sodium Thiosulfate in Animal Models Reduces Platinum Ototoxity wihtout Reduction of Antitumor Activity,” Clinical Cancer Research. 6(1): 309-315 (2000). [cited by applicant]
Naert et al., “Use of the guinea pig in studies on the development and prevention of acquired sensorineural hearing loss, with an emphasis on noise,” J Acoust Soc Am. 146(5): 3743-69 (Nov. 2019) (28 pages). [cited by applicant]
Otto et al., “Effects of cisplatin and thiosulfate upon auditory brainstem responses of guinea pigs,” Hear Res. 35(1):79-85 (1988). [cited by applicant]
Pestieau et al., “Impact of carrier solutions on pharmacokinetics of intraperitoneal chemotherapy,” Cancer Chemother Pharmacol. 47(3):269-76 (2001) (Abstract Only) (2 pages). [cited by applicant]
Pierre et al., “Middle ear administration of a particulate chitosan gel in an in vivo model of cisplatin ototoxicity,” Front Cell Neurosci. 13(268): (Jun. 2019) (13 pages). [cited by applicant]
Pierre, Pernilla, Thesis: “Cisplatin, a platinum-containing antineoplastic drug: perspectives on analytical chemistry and prevention of ototoxicity,” Department of Oncology-Pathology, Karolinska Institutet, 2010. [cited by applicant]
Rolland et al., “A randomized controlled trial to test the efficacy of trans-tympanic injections of a sodium thiosulfate gel to prevent cisplatin-induced ototoxicity in patients with head and neck cancer,” J Otolaryngol… [cited by applicant]
Togawa et al., “High performance liquid chromatographic determination of bound sulfide and sulfite and thiosulfate at their low levels in human serum by pre-col. fluorescence derivatization with monobromobimane,” Chem P… [cited by applicant]
Urien et al., “Population pharmacokinetics of total and unbound plasma cisplatin in adult patients,” Br J Clin Pharmacol. 57(6):756-63 (2004). [cited by applicant]
Wang et al., “Local application of sodium thiosulfate prevents cisplatin-induced hearing loss in the guinea pig,” Neuropharmacology. 45(3):380-93 (2003). [cited by applicant]
Wang, “Tolerability of hypertonic injectables,” Int J Pharm. 490(1-2):308-15 (2015). [cited by applicant]
Wu et al., “The chemoprotective agent N-acetylcysteine blocks cisplatin-induced apoptosis through caspase signaling pathway,” J Pharmacol Exp Ther 312(2):424-31 (2005). [cited by applicant]