CS1 targeted chimeric antigen receptor-modified T cells
Chimeric antigen receptors for use in treating malignant melanoma and other cancers expressing CS1 are described.
1 . A nucleic acid molecule comprising a nucleotide sequence encoding a chimeric antigen receptor (CAR) targeting CS1, wherein the CAR comprises:
(a) a CS1 scFv comprising the amino acid sequence of SEQ ID NO: 1; a spacer domain comprising the amino acid sequence of SEQ ID NO: 9; a transmembrane domain comprising the amino acid sequence of SEQ ID NO: 15; a co-signaling domain comprising the amino acid sequence of SEQ ID NO: 23; and a CD3ζ signaling domain comprising the amino acid sequence of SEQ ID NO: 21;
(b) a CS1 scFv comprising the amino acid sequence of SEQ ID NO: 1; a spacer domain comprising the amino acid sequence of SEQ ID NO: 9; a transmembrane domain comprising the amino acid sequence of SEQ ID NO: 16; a co-signaling domain comprising the amino acid sequence of SEQ ID NO: 24; and a CD3ζ signaling domain comprising the amino acid sequence of SEQ ID NO: 21;
(c) a CS1 scFv comprising the amino acid sequence of SEQ ID NO: 1; a spacer domain comprising the amino acid sequence of SEQ ID NO: 11; a transmembrane domain comprising the amino acid sequence of SEQ ID NO: 16; a co-signaling domain comprising the amino acid sequence of SEQ ID NO: 24; and a CD3ζ signaling domain comprising the amino acid sequence of SEQ ID NO: 21;
(d) a CS1 scFv comprising the amino acid sequence of SEQ ID NO: 1; a spacer domain comprising the amino acid sequence of SEQ ID NO: 11; a transmembrane domain comprising the amino acid sequence of SEQ ID NO: 15; a co-signaling domain comprising the amino acid sequence of SEQ ID NO: 23; and a CD3ζ signaling domain comprising the amino acid sequence of SEQ ID NO: 21;
(e) a CS1 scFv comprising the amino acid sequence of SEQ ID NO: 1; a spacer domain comprising the amino acid sequence of SEQ ID NO: 2; a transmembrane domain comprising the amino acid sequence of SEQ ID NO: 16; a co-signaling domain comprising the amino acid sequence of SEQ ID NO: 24; and a CD3ζ signaling domain comprising the amino acid sequence of SEQ ID NO: 21; or
(f) a CS1 scFv comprising the amino acid sequence of SEQ ID NO: 1; a spacer domain comprising the amino acid sequence of SEQ ID NO: 2; a transmembrane domain comprising the amino acid sequence of SEQ ID NO: 15; a co-signaling domain comprising the amino acid sequence of SEQ ID NO: 23; and a CD3ζ signaling domain comprising the amino acid sequence of SEQ ID NO: 21.
2 . The nucleic acid molecule of claim 1 , wherein the CAR comprises:
(a) a CS1 scFv consisting of the amino acid sequence of SEQ ID NO: 1; a spacer domain consisting of the amino acid sequence of SEQ ID NO: 9; a transmembrane domain consisting of the amino acid sequence of SEQ ID NO: 15; a co-signaling domain consisting of the amino acid sequence of SEQ ID NO: 23; and a CD3ζ signaling domain consisting of the amino acid sequence of SEQ ID NO: 21;
(b) a CS1 scFv consisting of the amino acid SEQ ID NO: 1; a spacer domain consisting of the amino acid sequence of SEQ ID NO: 9; a transmembrane domain consisting of the amino acid sequence of SEQ ID NO: 16; a co-signaling domain consisting of the amino acid sequence of SEQ ID NO: 24; and a CD3ζ signaling domain consisting of the amino acid sequence of SEQ ID NO: 21;
(c) a CS1 scFv consisting of the amino acid sequence of SEQ ID NO: 1; a spacer domain consisting of the amino acid sequence of SEQ ID NO: 11; a transmembrane domain consisting of the amino acid sequence of SEQ ID NO: 16; a co-signaling domain consisting of the amino acid sequence of SEQ ID NO: 24; and a CD3ζ signaling domain consisting of the amino acid sequence of SEQ ID NO: 21;
(d) a CS1 scFv consisting of the amino acid sequence of SEQ ID NO: 1; a spacer domain consisting of the amino acid sequence of SEQ ID NO: 11; a transmembrane domain consisting of the amino acid sequence of SEQ ID NO: 15; a co-signaling domain consisting of the amino acid sequence of SEQ ID NO: 23; and a CD3ζ signaling domain consisting of the amino acid sequence of SEQ ID NO: 21;
(e) a CS1 scFv consisting of the amino acid sequence of SEQ ID NO: 1; a spacer domain consisting of the amino acid sequence of SEQ ID NO: 2; a transmembrane domain consisting of the amino acid sequence of SEQ ID NO: 16; a co-signaling domain consisting of the amino acid sequence of SEQ ID NO: 24; and a CD3ζ signaling domain consisting of the amino acid sequence of SEQ ID NO: 21; or
(f) a CS1 scFv consisting of the amino acid sequence of SEQ ID NO: 1; a spacer domain consisting of the amino acid sequence of SEQ ID NO: 2; a transmembrane domain consisting of the amino acid sequence of SEQ ID NO: 15; a co-signaling domain consisting of the amino acid sequence of SEQ ID NO: 23; and a CD3ζ signaling domain consisting of the amino acid sequence of SEQ ID NO: 21.
3 . A population of human T cells harboring the nucleic acid molecule of claim 1 .
4 . The population of human T cells of claim 3 , wherein at least 20%, 30%, 40%, 50%, 60%, 70% or 80% of the transduced human T cells are central memory T cells.
5 . The population of human T cells of claim 4 , wherein at least 10% or 20% of the transduced central memory T cells are CD4+.
6 . The population of human T cells of claim 4 , wherein at least 10% or 20% of the transduced central memory T cells are CD8+.
7 . The population of human T cells of claim 4 , wherein at least 10% of the central memory T cells are CD4+ and at least 10% are CD8+.
8 . The population of human T cells of claim 7 , wherein at least 30% of the transduced human T cells are central memory T cells.
9 . A population of human T cells harboring the nucleic acid molecule of claim 2 .
10 . The population of human T cells of claim 9 , wherein at least 20%, 30%, 40%, 50%, 60%, 70% or 80% of the transduced human T cells are central memory T cells.
11 . The population of human T cells of claim 10 , wherein at least 10% or 20% of the transduced central memory T cells are CD4+.
12 . The population of human T cells of claim 10 , wherein at least 10% or 20% of the transduced central memory T cells are CD8+.
13 . The population of human T cells of claim 10 , wherein at least 10% of the central memory T cells are CD4+ and at least 10% are CD8+.
14 . The population of human T cells of claim 13 , wherein at least 30% of the transduced human T cells are central memory T cells.